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Global Spinal Muscular Atrophy (SMA) Therapeutic Market Research Report 2026(Status and Outlook)

Publisher Bosson Research
Published Jan 01, 2026
Length 130 Pages
SKU # BOSS20845422

Description

Report Overview

Spinal muscular atrophy treatment market growth is driven by a significant increase in the number of product launches despite the relative rarity of the disorder and high costs associated with the approved drugs. The treatment of spinal muscular atrophy through the gene therapy drug called ZolgensmaThe global pharmaceutical market is 1475 billion USD in 2022, growing at a CAGR of 5% during the next six years. The pharmaceutical market includes chemical drugs and biological drugs. For biologics is expected to 381 billion USD in 2022. In comparison, the chemical drug market is estimated to increase from 1005 billion in 2018 to 1094 billion U.S. dollars in 2022. The pharmaceutical market factors such as increasing demand for healthcare, technological advancements, and the rising prevalence of chronic diseases, increase in funding from private & government organizations for development of pharmaceutical manufacturing segments and rise in R&D activities for drugs. However, the industry also faces challenges such as stringent regulations, high costs of research and development, and patent expirations. Companies need to continuously innovate and adapt to these challenges to stay competitive in the market and ensure their products reach patients in need. Additionally, the COVID-19 pandemic has highlighted the importance of vaccine development and supply chain management, further emphasizing the need for pharmaceutical companies to be agile and responsive to emerging public health needs.

The global Spinal Muscular Atrophy (SMA) Therapeutic market size was estimated at USD 5361.0 million in 2025 and is projected to grow at a compound annual growth rate (CAGR) of 18.00% during the forecast period.

This report offers a comprehensive and in-depth analysis of the global Spinal Muscular Atrophy (SMA) Therapeutic market, covering all critical facets from a broad macroeconomic overview to detailed micro-level insights. It examines market size, competitive landscape, emerging development trends, niche segments, key drivers and challenges, as well as conducts SWOT and value chain analyses.

The insights provided enable readers to understand the competitive dynamics within the industry and formulate effective strategies to enhance profitability and market positioning. Additionally, the report presents a clear framework for evaluating the current status and future outlook of business organizations operating in this sector.

A significant focus of this report lies in the competitive landscape of the global Spinal Muscular Atrophy (SMA) Therapeutic market. It offers detailed profiles of major players, including their market shares, performance metrics, product portfolios, and operational status. This enables stakeholders to identify leading competitors and gain a nuanced understanding of market rivalry and structure.

In summary, this report serves as an essential resource for industry participants, investors, researchers, consultants, and business strategists, as well as anyone planning to enter or expand their presence in the Spinal Muscular Atrophy (SMA) Therapeutic market.

Global Spinal Muscular Atrophy (SMA) Therapeutic Market: Market Segmentation Analysis

This research report provides a detailed segmentation of the market by region (country), key manufacturers, product type, and application. Market segmentation divides the overall market into distinct subsets based on factors such as product categories, end-user industries, geographic locations, and other relevant criteria.

A clear understanding of these market segments enables decision-makers to tailor their product development, sales, and marketing strategies more effectively to meet the unique needs of each segment. Leveraging market segmentation insights can significantly enhance targeted approaches, optimize resource allocation, and accelerate product innovation cycles by aligning offerings with the specific demands of diverse customer groups.

Key Company

Biogen

Novartis

Roche

Astellas Pharma

Genzyme Corporation

Market Segmentation (by Type)

Nusinersen

Onasemnogen Abeparvovec

Market Segmentation (by Application)

Type 1 SMA

Type 2 SMA

Other

Geographic Segmentation

North America (USA, Canada, Mexico)

Europe (Germany, UK, France, Russia, Italy, Rest of Europe)

Asia-Pacific (China, Japan, South Korea, India, Southeast Asia, Rest of Asia-Pacific)

South America (Brazil, Argentina, Columbia, Rest of South America)

The Middle East and Africa (Saudi Arabia, UAE, Egypt, Nigeria, South Africa, Rest of MEA)

Key Benefits of This Market Research:

Industry drivers, restraints, and opportunities covered in the study

Neutral perspective on the market performance

Recent industry trends and developments

Competitive landscape & strategies of key players

Potential & niche segments and regions exhibiting promising growth covered

Historical, current, and projected market size, in terms of value

In-depth analysis of the Spinal Muscular Atrophy (SMA) Therapeutic Market

Overview of the regional outlook of the Spinal Muscular Atrophy (SMA) Therapeutic Market:

Chapter Outline

Chapter 1 mainly introduces the statistical scope of the report, market division standards, and market research methods.

Chapter 2 is an executive summary of different market segments (by region, product type, application, etc), including the market size of each market segment, future development potential, and so on. It offers a high-level view of the current state of the Spinal Muscular Atrophy (SMA) Therapeutic Market and its likely evolution in the short to mid-term, and long term.

Chapter 3 makes a detailed analysis of the market's competitive landscape of the market and provides the market share, capacity, output, price, latest development plan, merger, and acquisition information of the main manufacturers in the market.

Chapter 4 is the analysis of the whole market industrial chain, including the upstream and downstream of the industry, as well as Porter's five forces analysis.

Chapter 5 introduces the latest developments of the market, the driving factors and restrictive factors of the market, the challenges and risks faced by manufacturers in the industry, and the analysis of relevant policies in the industry.

Chapter 6 provides the analysis of various market segments according to product types, covering the market size and development potential of each market segment, to help readers find the blue ocean market in different market segments.

Chapter 7 provides the analysis of various market segments according to application, covering the market size and development potential of each market segment, to help readers find the blue ocean market in different downstream markets.

Chapter 8 provides a quantitative analysis of the market size and development potential of each region and its main countries and introduces the market development, future development prospects, market space, and capacity of each country in the world.

Chapter 9 shares the main producing countries of Spinal Muscular Atrophy (SMA) Therapeutic, their output value, profit level, regional supply, production capacity layout, etc. from the supply side.

Chapter 10 introduces the basic situation of the main companies in the market in detail, including product sales revenue, sales volume, price, gross profit margin, market share, product introduction, recent development, etc.

Chapter 11 provides a quantitative analysis of the market size and development potential of each region in the next five years.

Chapter 12 provides a quantitative analysis of the market size and development potential of each market segment in the next five years.

Chapter 13 is the main points and conclusions of the report.

Key Reasons to Buy this Report:

Access to date statistics compiled by our researchers. These provide you with historical and forecast data, which is analyzed to tell you why your market is set to change

This enables you to anticipate market changes to remain ahead of your competitors

You will be able to copy data from the Excel spreadsheet straight into your marketing plans, business presentations, or other strategic documents

The concise analysis, clear graph, and table format will enable you to pinpoint the information you require quickly

Provision of market value data for each segment and sub-segment

Indicates the region and segment that is expected to witness the fastest growth as well as to dominate the market

Analysis by geography highlighting the consumption of the product/service in the region as well as indicating the factors that are affecting the market within each region

Competitive landscape which incorporates the market ranking of the major players, along with new service/product launches, partnerships, business expansions, and acquisitions in the past five years of companies profiled

Extensive company profiles comprising of company overview, company insights, product benchmarking, and SWOT analysis for the major market players

The current as well as the future market outlook of the industry concerning recent developments which involve growth opportunities and drivers as well as challenges and restraints of both emerging as well as developed regions

Includes in-depth analysis of the market from various perspectives through Porter’s five forces analysis

Provides insight into the market through Value Chain

Market dynamics scenario, along with growth opportunities of the market in the years to come

Table of Contents

130 Pages
1 Research Methodology and Statistical Scope
1.1 Market Definition and Statistical Scope of Spinal Muscular Atrophy (SMA) Therapeutic
1.2 Key Market Segments
1.2.1 Spinal Muscular Atrophy (SMA) Therapeutic Segment by Type
1.2.2 Spinal Muscular Atrophy (SMA) Therapeutic Segment by Application
1.3 Methodology & Sources of Information
1.3.1 Research Methodology
1.3.2 Research Process
1.3.3 Market Breakdown and Data Triangulation
1.3.4 Base Year
1.3.5 Report Assumptions & Caveats
2 Spinal Muscular Atrophy (SMA) Therapeutic Market Overview
2.1 Global Market Overview
2.1.1 Global Spinal Muscular Atrophy (SMA) Therapeutic Market Size (M USD) Estimates and Forecasts (2020-2035)
2.1.2 Global Spinal Muscular Atrophy (SMA) Therapeutic Sales Estimates and Forecasts (2020-2035)
2.2 Market Segment Executive Summary
2.3 Global Market Size by Region
3 Spinal Muscular Atrophy (SMA) Therapeutic Market Competitive Landscape
3.1 Company Assessment Quadrant
3.2 Global Spinal Muscular Atrophy (SMA) Therapeutic Product Life Cycle
3.3 Global Spinal Muscular Atrophy (SMA) Therapeutic Sales by Manufacturers (2020-2025)
3.4 Global Spinal Muscular Atrophy (SMA) Therapeutic Revenue Market Share by Manufacturers (2020-2025)
3.5 Spinal Muscular Atrophy (SMA) Therapeutic Market Share by Company Type (Tier 1, Tier 2, and Tier 3)
3.6 Global Spinal Muscular Atrophy (SMA) Therapeutic Average Price by Manufacturers (2020-2025)
3.7 Manufacturers’ Manufacturing Sites, Areas Served, and Product Types
3.8 Spinal Muscular Atrophy (SMA) Therapeutic Market Competitive Situation and Trends
3.8.1 Spinal Muscular Atrophy (SMA) Therapeutic Market Concentration Rate
3.8.2 Global 5 and 10 Largest Spinal Muscular Atrophy (SMA) Therapeutic Players Market Share by Revenue
3.8.3 Mergers & Acquisitions, Expansion
4 Spinal Muscular Atrophy (SMA) Therapeutic Industry Chain Analysis
4.1 Spinal Muscular Atrophy (SMA) Therapeutic Industry Chain Analysis
4.2 Market Overview of Key Raw Materials
4.3 Midstream Market Analysis
4.4 Downstream Customer Analysis
5 The Development and Dynamics of Spinal Muscular Atrophy (SMA) Therapeutic Market
5.1 Key Development Trends
5.2 Driving Factors
5.3 Market Challenges
5.4 Industry News
5.4.1 New Product Developments
5.4.2 Mergers & Acquisitions
5.4.3 Expansions
5.4.4 Collaboration/Supply Contracts
5.5 PEST Analysis
5.5.1 Industry Policies Analysis
5.5.2 Economic Environment Analysis
5.5.3 Social Environment Analysis
5.5.4 Technological Environment Analysis
5.6 Global Spinal Muscular Atrophy (SMA) Therapeutic Market Porter's Five Forces Analysis
5.6.1 Global Trade Frictions
5.6.2 U.S. Tariff Policy – April 2025
5.6.3 Global Trade Frictions and Their Impacts to Spinal Muscular Atrophy (SMA) Therapeutic Market
5.7 ESG Ratings of Leading Companies
6 Spinal Muscular Atrophy (SMA) Therapeutic Market Segmentation by Type
6.1 Evaluation Matrix of Segment Market Development Potential (Type)
6.2 Global Spinal Muscular Atrophy (SMA) Therapeutic Sales Market Share by Type (2020-2025)
6.3 Global Spinal Muscular Atrophy (SMA) Therapeutic Market Size by Type (2020-2025)
6.4 Global Spinal Muscular Atrophy (SMA) Therapeutic Price by Type (2020-2025)
7 Spinal Muscular Atrophy (SMA) Therapeutic Market Segmentation by Application
7.1 Evaluation Matrix of Segment Market Development Potential (Application)
7.2 Global Spinal Muscular Atrophy (SMA) Therapeutic Market Sales by Application (2020-2025)
7.3 Global Spinal Muscular Atrophy (SMA) Therapeutic Market Size (M USD) by Application (2020-2025)
7.4 Global Spinal Muscular Atrophy (SMA) Therapeutic Sales Growth Rate by Application (2020-2025)
8 Spinal Muscular Atrophy (SMA) Therapeutic Market Sales by Region
8.1 Global Spinal Muscular Atrophy (SMA) Therapeutic Sales by Region
8.1.1 Global Spinal Muscular Atrophy (SMA) Therapeutic Sales by Region
8.1.2 Global Spinal Muscular Atrophy (SMA) Therapeutic Sales Market Share by Region
8.2 Global Spinal Muscular Atrophy (SMA) Therapeutic Market Size by Region
8.2.1 Global Spinal Muscular Atrophy (SMA) Therapeutic Market Size by Region
8.2.2 Global Spinal Muscular Atrophy (SMA) Therapeutic Market Size by Region
8.3 North America
8.3.1 North America Spinal Muscular Atrophy (SMA) Therapeutic Sales by Country
8.3.2 North America Spinal Muscular Atrophy (SMA) Therapeutic Market Size by Country
8.3.3 U.S. Market Overview
8.3.4 Canada Market Overview
8.3.5 Mexico Market Overview
8.4 Europe
8.4.1 Europe Spinal Muscular Atrophy (SMA) Therapeutic Sales by Country
8.4.2 Europe Spinal Muscular Atrophy (SMA) Therapeutic Market Size by Country
8.4.3 Germany Market Overview
8.4.4 France Market Overview
8.4.5 U.K. Market Overview
8.4.6 Italy Market Overview
8.4.7 Spain Market Overview
8.5 Asia Pacific
8.5.1 Asia Pacific Spinal Muscular Atrophy (SMA) Therapeutic Sales by Region
8.5.2 Asia Pacific Spinal Muscular Atrophy (SMA) Therapeutic Market Size by Region
8.5.3 China Market Overview
8.5.4 Japan Market Overview
8.5.5 South Korea Market Overview
8.5.6 India Market Overview
8.5.7 Southeast Asia Market Overview
8.6 South America
8.6.1 South America Spinal Muscular Atrophy (SMA) Therapeutic Sales by Country
8.6.2 South America Spinal Muscular Atrophy (SMA) Therapeutic Market Size by Country
8.6.3 Brazil Market Overview
8.6.4 Argentina Market Overview
8.6.5 Columbia Market Overview
8.7 Middle East and Africa
8.7.1 Middle East and Africa Spinal Muscular Atrophy (SMA) Therapeutic Sales by Region
8.7.2 Middle East and Africa Spinal Muscular Atrophy (SMA) Therapeutic Market Size by Region
8.7.3 Saudi Arabia Market Overview
8.7.4 UAE Market Overview
8.7.5 Egypt Market Overview
8.7.6 Nigeria Market Overview
8.7.7 South Africa Market Overview
9 Spinal Muscular Atrophy (SMA) Therapeutic Market Production by Region
9.1 Global Production of Spinal Muscular Atrophy (SMA) Therapeutic by Region(2020-2025)
9.2 Global Spinal Muscular Atrophy (SMA) Therapeutic Revenue Market Share by Region (2020-2025)
9.3 Global Spinal Muscular Atrophy (SMA) Therapeutic Production, Revenue, Price and Gross Margin (2020-2025)
9.4 North America Spinal Muscular Atrophy (SMA) Therapeutic Production
9.4.1 North America Spinal Muscular Atrophy (SMA) Therapeutic Production Growth Rate (2020-2025)
9.4.2 North America Spinal Muscular Atrophy (SMA) Therapeutic Production, Revenue, Price and Gross Margin (2020-2025)
9.5 Europe Spinal Muscular Atrophy (SMA) Therapeutic Production
9.5.1 Europe Spinal Muscular Atrophy (SMA) Therapeutic Production Growth Rate (2020-2025)
9.5.2 Europe Spinal Muscular Atrophy (SMA) Therapeutic Production, Revenue, Price and Gross Margin (2020-2025)
9.6 Japan Spinal Muscular Atrophy (SMA) Therapeutic Production (2020-2025)
9.6.1 Japan Spinal Muscular Atrophy (SMA) Therapeutic Production Growth Rate (2020-2025)
9.6.2 Japan Spinal Muscular Atrophy (SMA) Therapeutic Production, Revenue, Price and Gross Margin (2020-2025)
9.7 China Spinal Muscular Atrophy (SMA) Therapeutic Production (2020-2025)
9.7.1 China Spinal Muscular Atrophy (SMA) Therapeutic Production Growth Rate (2020-2025)
9.7.2 China Spinal Muscular Atrophy (SMA) Therapeutic Production, Revenue, Price and Gross Margin (2020-2025)
10 Key Companies Profile
10.1 Biogen
10.1.1 Biogen Basic Information
10.1.2 Biogen Spinal Muscular Atrophy (SMA) Therapeutic Product Overview
10.1.3 Biogen Spinal Muscular Atrophy (SMA) Therapeutic Product Market Performance
10.1.4 Biogen Business Overview
10.1.5 Biogen SWOT Analysis
10.1.6 Biogen Recent Developments
10.2 Novartis
10.2.1 Novartis Basic Information
10.2.2 Novartis Spinal Muscular Atrophy (SMA) Therapeutic Product Overview
10.2.3 Novartis Spinal Muscular Atrophy (SMA) Therapeutic Product Market Performance
10.2.4 Novartis Business Overview
10.2.5 Novartis SWOT Analysis
10.2.6 Novartis Recent Developments
10.3 Roche
10.3.1 Roche Basic Information
10.3.2 Roche Spinal Muscular Atrophy (SMA) Therapeutic Product Overview
10.3.3 Roche Spinal Muscular Atrophy (SMA) Therapeutic Product Market Performance
10.3.4 Roche Business Overview
10.3.5 Roche SWOT Analysis
10.3.6 Roche Recent Developments
10.4 Astellas Pharma
10.4.1 Astellas Pharma Basic Information
10.4.2 Astellas Pharma Spinal Muscular Atrophy (SMA) Therapeutic Product Overview
10.4.3 Astellas Pharma Spinal Muscular Atrophy (SMA) Therapeutic Product Market Performance
10.4.4 Astellas Pharma Business Overview
10.4.5 Astellas Pharma Recent Developments
10.5 Genzyme Corporation
10.5.1 Genzyme Corporation Basic Information
10.5.2 Genzyme Corporation Spinal Muscular Atrophy (SMA) Therapeutic Product Overview
10.5.3 Genzyme Corporation Spinal Muscular Atrophy (SMA) Therapeutic Product Market Performance
10.5.4 Genzyme Corporation Business Overview
10.5.5 Genzyme Corporation Recent Developments
11 Spinal Muscular Atrophy (SMA) Therapeutic Market Forecast by Region
11.1 Global Spinal Muscular Atrophy (SMA) Therapeutic Market Size Forecast
11.2 Global Spinal Muscular Atrophy (SMA) Therapeutic Market Forecast by Region
11.2.1 North America Market Size Forecast by Country
11.2.2 Europe Spinal Muscular Atrophy (SMA) Therapeutic Market Size Forecast by Country
11.2.3 Asia Pacific Spinal Muscular Atrophy (SMA) Therapeutic Market Size Forecast by Region
11.2.4 South America Spinal Muscular Atrophy (SMA) Therapeutic Market Size Forecast by Country
11.2.5 Middle East and Africa Forecasted Sales of Spinal Muscular Atrophy (SMA) Therapeutic by Country
12 Forecast Market by Type and by Application (2026-2035)
12.1 Global Spinal Muscular Atrophy (SMA) Therapeutic Market Forecast by Type (2026-2035)
12.1.1 Global Forecasted Sales of Spinal Muscular Atrophy (SMA) Therapeutic by Type (2026-2035)
12.1.2 Global Spinal Muscular Atrophy (SMA) Therapeutic Market Size Forecast by Type (2026-2035)
12.1.3 Global Forecasted Price of Spinal Muscular Atrophy (SMA) Therapeutic by Type (2026-2035)
12.2 Global Spinal Muscular Atrophy (SMA) Therapeutic Market Forecast by Application (2026-2035)
12.2.1 Global Spinal Muscular Atrophy (SMA) Therapeutic Sales (K Units) Forecast by Application
12.2.2 Global Spinal Muscular Atrophy (SMA) Therapeutic Market Size (M USD) Forecast by Application (2026-2035)
13 Conclusion and Key Findings
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