
Spinal Muscular Atrophy (SMA) Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update
Description
Spinal Muscular Atrophy (SMA) Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update
Summary
Global Markets Direct's latest Pharmaceutical and Healthcare disease pipeline guide Spinal Muscular Atrophy (SMA) - Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update, provides an overview of the Spinal Muscular Atrophy (SMA) (Central Nervous System) pipeline landscape.
Spinal muscular atrophy (SMA) is a genetic disease that attacks nerve cells, called motor neurons, in the spinal cord. These critically important cells are responsible for supplying electrical and chemical messages to muscle cells. Without the proper input from the motor neurons, muscle cells cannot function properly. The muscle cells will, therefore, become much smaller (atrophy) and will produce symptoms of muscle weakness. This can affect walking, crawling, breathing, swallowing, and head and neck control.
Report Highlights
Global Markets Direct's Pharmaceutical and Healthcare latest pipeline guide Spinal Muscular Atrophy (SMA) - Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update, provides comprehensive information on the therapeutics under development for Spinal Muscular Atrophy (SMA) (Central Nervous System), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.
The Spinal Muscular Atrophy (SMA) (Central Nervous System) pipeline guide also reviews of key players involved in therapeutic development for Spinal Muscular Atrophy (SMA) and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Pre-Registration, Phase III, Phase II, Phase I, IND/CTA Filed, Preclinical, Discovery and Unknown stages are 2, 1, 5, 5, 1, 23, 9 and 1 respectively. Similarly, the Universities portfolio in Phase II, Preclinical and Discovery stages comprises 2, 8 and 2 molecules, respectively.
Spinal Muscular Atrophy (SMA) (Central Nervous System) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from Global Markets Direct’s proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.
Note:Certain content / sections in the pipeline guide may be removed or altered based on the availability and relevance of data.
Scope
Summary
Global Markets Direct's latest Pharmaceutical and Healthcare disease pipeline guide Spinal Muscular Atrophy (SMA) - Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update, provides an overview of the Spinal Muscular Atrophy (SMA) (Central Nervous System) pipeline landscape.
Spinal muscular atrophy (SMA) is a genetic disease that attacks nerve cells, called motor neurons, in the spinal cord. These critically important cells are responsible for supplying electrical and chemical messages to muscle cells. Without the proper input from the motor neurons, muscle cells cannot function properly. The muscle cells will, therefore, become much smaller (atrophy) and will produce symptoms of muscle weakness. This can affect walking, crawling, breathing, swallowing, and head and neck control.
Report Highlights
Global Markets Direct's Pharmaceutical and Healthcare latest pipeline guide Spinal Muscular Atrophy (SMA) - Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update, provides comprehensive information on the therapeutics under development for Spinal Muscular Atrophy (SMA) (Central Nervous System), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.
The Spinal Muscular Atrophy (SMA) (Central Nervous System) pipeline guide also reviews of key players involved in therapeutic development for Spinal Muscular Atrophy (SMA) and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Pre-Registration, Phase III, Phase II, Phase I, IND/CTA Filed, Preclinical, Discovery and Unknown stages are 2, 1, 5, 5, 1, 23, 9 and 1 respectively. Similarly, the Universities portfolio in Phase II, Preclinical and Discovery stages comprises 2, 8 and 2 molecules, respectively.
Spinal Muscular Atrophy (SMA) (Central Nervous System) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from Global Markets Direct’s proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.
Note:Certain content / sections in the pipeline guide may be removed or altered based on the availability and relevance of data.
Scope
- The pipeline guide provides a snapshot of the global therapeutic landscape of Spinal Muscular Atrophy (SMA) (Central Nervous System).
- The pipeline guide reviews pipeline therapeutics for Spinal Muscular Atrophy (SMA) (Central Nervous System) by companies and universities/research institutes based on information derived from company and industry-specific sources.
- The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.
- The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.
- The pipeline guide reviews key companies involved in Spinal Muscular Atrophy (SMA) (Central Nervous System) therapeutics and enlists all their major and minor projects.
- The pipeline guide evaluates Spinal Muscular Atrophy (SMA) (Central Nervous System) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA) and molecule type.
- The pipeline guide encapsulates all the dormant and discontinued pipeline projects.
- The pipeline guide reviews latest news related to pipeline therapeutics for Spinal Muscular Atrophy (SMA) (Central Nervous System)
- Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.
- Recognize emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage.
- Find and recognize significant and varied types of therapeutics under development for Spinal Muscular Atrophy (SMA) (Central Nervous System).
- Classify potential new clients or partners in the target demographic.
- Develop tactical initiatives by understanding the focus areas of leading companies.
- Plan mergers and acquisitions meritoriously by identifying key players and it’s most promising pipeline therapeutics.
- Formulate corrective measures for pipeline projects by understanding Spinal Muscular Atrophy (SMA) (Central Nervous System) pipeline depth and focus of Indication therapeutics.
- Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.
- Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from pipeline.
Companies Mentioned
Companies Mentioned
Alcyone Therapeutics Inc
AlphaCognition Inc
Amniotics AB
Anima Biotech Inc
Annji Pharmaceutical Co Ltd
Apteeus SAS
ARMGO Pharma Inc
Beijing GeneCradle Technology Co Ltd
Biocad
Biogen Inc
Biohaven Pharmaceutical Holding Company Ltd
Bioleaders Corp
BioMarin Pharmaceutical Inc
Biophytis SA
Cell Tech Pharmed Co
Chugai Pharmaceutical Co Ltd
Enzerna Biosciences LLC
Exegenesis Bio Inc
F. Hoffmann-La Roche Ltd
Genentech USA Inc
GNT Pharma Co Ltd
Huida (Shanghai) Biotechnology Co Ltd
Imago Pharmaceuticals Inc
Myocea Inc
Neurotune AG
NMD Pharma AS
Novartis AG
Novartis Gene Therapies
Oncternal Therapeutics
Ono Pharmaceutical Co Ltd
PTC Therapeutics Inc
Ractigen Therapeutics Inc
Reborna Biosciences Inc
Sarepta Therapeutics Inc
Scholar Rock Inc
Shift Pharmaceuticals
Spotlight Innovation Inc
Suzhou GenAssist Therapeutics Co Ltd
Voyager Therapeutics Inc
Vybion Inc
Companies Mentioned
Alcyone Therapeutics Inc
AlphaCognition Inc
Amniotics AB
Anima Biotech Inc
Annji Pharmaceutical Co Ltd
Apteeus SAS
ARMGO Pharma Inc
Beijing GeneCradle Technology Co Ltd
Biocad
Biogen Inc
Biohaven Pharmaceutical Holding Company Ltd
Bioleaders Corp
BioMarin Pharmaceutical Inc
Biophytis SA
Cell Tech Pharmed Co
Chugai Pharmaceutical Co Ltd
Enzerna Biosciences LLC
Exegenesis Bio Inc
F. Hoffmann-La Roche Ltd
Genentech USA Inc
GNT Pharma Co Ltd
Huida (Shanghai) Biotechnology Co Ltd
Imago Pharmaceuticals Inc
Myocea Inc
Neurotune AG
NMD Pharma AS
Novartis AG
Novartis Gene Therapies
Oncternal Therapeutics
Ono Pharmaceutical Co Ltd
PTC Therapeutics Inc
Ractigen Therapeutics Inc
Reborna Biosciences Inc
Sarepta Therapeutics Inc
Scholar Rock Inc
Shift Pharmaceuticals
Spotlight Innovation Inc
Suzhou GenAssist Therapeutics Co Ltd
Voyager Therapeutics Inc
Vybion Inc
Table of Contents
139 Pages
- Introduction
- Global Markets Direct Report Coverage
- Spinal Muscular Atrophy (SMA) - Overview
- Spinal Muscular Atrophy (SMA) - Therapeutics Development
- Pipeline Overview
- Pipeline by Companies
- Pipeline by Universities/Institutes
- Products under Development by Companies
- Products under Development by Universities/Institutes
- Spinal Muscular Atrophy (SMA) - Therapeutics Assessment
- Assessment by Target
- Assessment by Mechanism of Action
- Assessment by Route of Administration
- Assessment by Molecule Type
- Spinal Muscular Atrophy (SMA) - Companies Involved in Therapeutics Development
- Alcyone Therapeutics Inc
- AlphaCognition Inc
- Amniotics AB
- Anima Biotech Inc
- Annji Pharmaceutical Co Ltd
- Apteeus SAS
- ARMGO Pharma Inc
- Beijing GeneCradle Technology Co Ltd
- Biocad
- Biogen Inc
- Biohaven Pharmaceutical Holding Company Ltd
- Bioleaders Corp
- BioMarin Pharmaceutical Inc
- Biophytis SA
- Cell Tech Pharmed Co
- Chugai Pharmaceutical Co Ltd
- Enzerna Biosciences LLC
- Exegenesis Bio Inc
- F. Hoffmann-La Roche Ltd
- Genentech USA Inc
- GNT Pharma Co Ltd
- Huida (Shanghai) Biotechnology Co Ltd
- Imago Pharmaceuticals Inc
- Myocea Inc
- Neurotune AG
- NMD Pharma AS
- Novartis AG
- Novartis Gene Therapies
- Oncternal Therapeutics
- Ono Pharmaceutical Co Ltd
- PTC Therapeutics Inc
- Ractigen Therapeutics Inc
- Reborna Biosciences Inc
- Sarepta Therapeutics Inc
- Scholar Rock Inc
- Shift Pharmaceuticals
- Spotlight Innovation Inc
- Suzhou GenAssist Therapeutics Co Ltd
- Voyager Therapeutics Inc
- Vybion Inc
- Spinal Muscular Atrophy (SMA) - Drug Profiles
- AAD-2004 - Drug Profile
- Product Description
- Mechanism Of Action
- ACTX-401 - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- ALB-111 - Drug Profile
- Product Description
- Mechanism Of Action
- ALPHA-0602 - Drug Profile
- Product Description
- Mechanism Of Action
- ALZ-002 - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- amifampridine phosphate - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- ANB-4 - Drug Profile
- Product Description
- Mechanism Of Action
- Antisense Oligonucleotide to Activate SMN2 for Spinal Muscular Atrophy - Drug Profile
- Product Description
- Mechanism Of Action
- Antisense Oligonucleotides for Spinal Muscular Atrophy - Drug Profile
- Product Description
- Mechanism Of Action
- apitegromab - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- ARM-210 - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- BIIB-089 - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- BIIB-110 - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- BIIB-115 - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- BIO-101 - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- BLSM-22 - Drug Profile
- Product Description
- Mechanism Of Action
- branaplam hydrochloride - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- CogniStem - Drug Profile
- Product Description
- Mechanism Of Action
- Drugs for Neuromuscular Diseases and Spinal Muscular Atrophy (SMA) - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- E-1V111 - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- ENZ-001 - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- GC-101 - Drug Profile
- Product Description
- Mechanism Of Action
- GEN-8010 - Drug Profile
- Product Description
- Mechanism Of Action
- Gene Therapies to Activate SMN1 for Spinal Muscular Atrophy - Drug Profile
- Product Description
- Mechanism Of Action
- Gene Therapy for Spinal Muscular Atrophy - Drug Profile
- Product Description
- Mechanism Of Action
- Gene Therapy to Activate SMN1 for Spinal Muscular Atrophy - Drug Profile
- Product Description
- Mechanism Of Action
- Gene Therapy to Activate SYT13 for Amyotrophic Lateral Sclerosis and Spinal Muscular Atrophy - Drug Profile
- Product Description
- Mechanism Of Action
- GTP-201 - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- GTx-505 - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- HG-001 - Drug Profile
- Product Description
- Mechanism Of Action
- INT-41 - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- maresin-1 - Drug Profile
- Product Description
- Mechanism Of Action
- Monoclonal Antibody to Inhibit Myostatin for Spinal Muscular Atrophy - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- NMDP-02 - Drug Profile
- Product Description
- Mechanism Of Action
- NT-1654 - Drug Profile
- Product Description
- Mechanism Of Action
- onasemnogene abeparvovec - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- ONCT-534 - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- PMO-25 - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- RAG-06 - Drug Profile
- Product Description
- Mechanism Of Action
- Resagen - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- RG-6237 - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- risdiplam - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Small Molecule for Spinal Muscular Atrophy - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Small Molecule to Inhibit GSK-3 for Spinal Muscular Atrophy - Drug Profile
- Product Description
- Mechanism Of Action
- Small Molecules 2 to Activate SMN2 for Spinal Muscular Atrophy - Drug Profile
- Product Description
- Mechanism Of Action
- Small Molecules for Central Nervous System Disorders - Drug Profile
- Product Description
- Mechanism Of Action
- Small Molecules for Kennedy's Disease - Drug Profile
- Product Description
- Mechanism Of Action
- Small Molecules for Spinal Muscular Atrophy - Drug Profile
- Product Description
- Mechanism Of Action
- Small Molecules for Spinal Muscular Atrophy - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Small Molecules for Spinal Muscular Atrophy - Drug Profile
- Product Description
- Mechanism Of Action
- Small Molecules to Activate SMN2 for Spinal Muscular Atrophy - Drug Profile
- Product Description
- Mechanism Of Action
- Small Molecules to Antagonize AR for Spinal and Bulbar Muscular Atrophy - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- STL-182 - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- talditercept alfa - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- TEC-1 - Drug Profile
- Product Description
- Mechanism Of Action
- TEE-375 - Drug Profile
- Product Description
- Mechanism Of Action
- TEE-703 - Drug Profile
- Product Description
- Mechanism Of Action
- timrepigene emparvovec - Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Vartocell - Drug Profile
- Product Description
- Mechanism Of Action
- Spinal Muscular Atrophy (SMA) - Dormant Projects
- Spinal Muscular Atrophy (SMA) - Discontinued Products
- Spinal Muscular Atrophy (SMA) - Product Development Milestones
- Featured News & Press Releases
- Mar 22, 2022: Scholar Rock presents data analysis of multiple efficacy endpoints from the apitegromab TOPAZ phase 2 trial at the American Academy of Neurology 2022 Annual Meeting
- Mar 16, 2022: New data for Roche’s Evrysdi (risdiplam) demonstrate long-term efficacy and safety in a broad population of people with spinal muscular atrophy (SMA)
- Mar 16, 2022: New data for Genentech’s Evrysdi (risdiplam) demonstrate long-term efficacy and safety in a broad population of people with Spinal Muscular Atrophy (SMA)
- Mar 13, 2022: Scholar Rock to present data from TOPAZ Ambulatory Cohort Analysis at the 2022 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference
- Mar 13, 2022: Novartis data again demonstrate age-appropriate development when Zolgensma is used presymptomatically, and post-hoc data reveal SMA Type 1 patients could speak, swallow and maintain airway protection
- Mar 08, 2022: Roche to present new Evrysdi data at MDA 2022 and highlight expanding neuromuscular disease portfolio
- Feb 03, 2022: Roche Canada and the pan-Canadian Pharmaceutical Alliance (pCPA) successfully complete negotiations for EVRYSDI (risdiplam) for the treatment of adults and children with spinal muscular atrophy (SMA)
- Jan 31, 2022: Cost-effectiveness analysis temporarily halted for Zolgensma to collect long-term data
- Jan 25, 2022: Roche’s Evrysdi (risdiplam) granted FDA priority review for treatment of pre-symptomatic babies under 2 months of age with spinal muscular atrophy (SMA)
- Nov 30, 2021: Scholar Rock announces design of phase 3 SAPPHIRE clinical trial evaluating apitegromab in non-ambulatory patients with Type 2 and Type 3 spinal muscular atrophy (SMA)
- Nov 19, 2021: NICE draft guidance recommends new treatment for spinal muscular atrophy as part of a managed access agreement
- Oct 19, 2021: Novartis applauds Quebec, the first province to list Zolgensma for the treatment of pediatric patients with spinal muscular atrophy (SMA)
- Oct 13, 2021: Novartis and the pan-Canadian Pharmaceutical Alliance (pCPA) complete negotiations for Zolgensma for the treatment of pediatric patients with spinal muscular atrophy (SMA)
- Oct 03, 2021: Scholar Rock to present Apitegromab TOPAZ phase 2 pharmacologic data at the 2021 World Congress of Neurology
- Sep 30, 2021: Scholar Rock presents exploratory responder analysis on efficacy data from the apitegromab TOPAZ phase 2 trial at the Child Neurology Society Annual Meeting
- Appendix
- Methodology
- Coverage
- Secondary Research
- Primary Research
- Expert Panel Validation
- Contact Us
- Disclaimer
- List of Tables
- Number of Products under Development for Spinal Muscular Atrophy (SMA), 2022
- Number of Products under Development by Companies, 2022
- Number of Products under Development by Companies, 2022 (Contd..1)
- Number of Products under Development by Universities/Institutes, 2022
- Products under Development by Companies, 2022
- Products under Development by Companies, 2022 (Contd..1)
- Products under Development by Companies, 2022 (Contd..2)
- Products under Development by Companies, 2022 (Contd..3)
- Products under Development by Universities/Institutes, 2022
- Number of Products by Stage and Target, 2022
- Number of Products by Stage and Mechanism of Action, 2022
- Number of Products by Stage and Route of Administration, 2022
- Number of Products by Stage and Molecule Type, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Alcyone Therapeutics Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by AlphaCognition Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Amniotics AB, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Anima Biotech Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Annji Pharmaceutical Co Ltd, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Apteeus SAS, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by ARMGO Pharma Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Beijing GeneCradle Technology Co Ltd, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Biocad, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Biogen Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Biohaven Pharmaceutical Holding Company Ltd, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Bioleaders Corp, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by BioMarin Pharmaceutical Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Biophytis SA, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Cell Tech Pharmed Co, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Chugai Pharmaceutical Co Ltd, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Enzerna Biosciences LLC, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Exegenesis Bio Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by F. Hoffmann-La Roche Ltd, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Genentech USA Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by GNT Pharma Co Ltd, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Huida (Shanghai) Biotechnology Co Ltd, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Imago Pharmaceuticals Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Myocea Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Neurotune AG, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by NMD Pharma AS, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Novartis AG, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Novartis Gene Therapies, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Oncternal Therapeutics, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Ono Pharmaceutical Co Ltd, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by PTC Therapeutics Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Ractigen Therapeutics Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Reborna Biosciences Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Sarepta Therapeutics Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Scholar Rock Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Shift Pharmaceuticals, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Spotlight Innovation Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Suzhou GenAssist Therapeutics Co Ltd, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Voyager Therapeutics Inc, 2022
- Spinal Muscular Atrophy (SMA) - Pipeline by Vybion Inc, 2022
- Spinal Muscular Atrophy (SMA) - Dormant Projects, 2022
- Spinal Muscular Atrophy (SMA) - Dormant Projects, 2022 (Contd..1)
- Spinal Muscular Atrophy (SMA) - Dormant Projects, 2022 (Contd..2)
- Spinal Muscular Atrophy (SMA) - Discontinued Products, 2022
- List of Figures
- Number of Products under Development for Spinal Muscular Atrophy (SMA), 2022
- Number of Products under Development by Companies, 2022
- Number of Products under Development by Universities/Institutes, 2022
- Number of Products by Top 10 Targets, 2022
- Number of Products by Stage and Top 10 Targets, 2022
- Number of Products by Top 10 Mechanism of Actions, 2022
- Number of Products by Stage and Top 10 Mechanism of Actions, 2022
- Number of Products by Routes of Administration, 2022
- Number of Products by Stage and Routes of Administration, 2022
- Number of Products by Top 10 Molecule Types, 2022
- Number of Products by Stage and Top 10 Molecule Types, 2022
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