
Duchenne Muscular Dystrophy Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update
Description
Duchenne Muscular Dystrophy Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update
Summary
Global Markets Direct's latest Pharmaceutical and Healthcare disease pipeline guide Duchenne Muscular Dystrophy - Drugs In Development, 2022, provides an overview of the Duchenne Muscular Dystrophy (Genetic Disorders) pipeline landscape.
Duchenne muscular dystrophy (DMD) is a genetic disorder that causes muscles to gradually weaken over time. Signs and symptoms of DMD include fatigue, learning difficulties, intellectual disability, muscle weakness and progressive difficulty walking. Risk factors include gender and family history. Treatment includes steroid medication, respiratory therapy and surgery.
Report Highlights
Global Markets Direct's Pharmaceutical and Healthcare latest pipeline guide Duchenne Muscular Dystrophy - Drugs In Development, 2022, provides comprehensive information on the therapeutics under development for Duchenne Muscular Dystrophy (Genetic Disorders), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.
The Duchenne Muscular Dystrophy (Genetic Disorders) pipeline guide also reviews of key players involved in therapeutic development for Duchenne Muscular Dystrophy and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Pre-Registration, Filing rejected/Withdrawn, Phase III, Phase II, Phase I, IND/CTA Filed, Preclinical, Discovery and Unknown stages are 1, 1, 7, 12, 15, 2, 71, 34 and 1 respectively. Similarly, the Universities portfolio in Phase III, Phase II, Phase I, IND/CTA Filed, Preclinical and Discovery stages comprises 2, 1, 2, 1, 13 and 3 molecules, respectively.
Duchenne Muscular Dystrophy (Genetic Disorders) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from Global Markets Direct’s proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.
Note: Certain content / sections in the pipeline guide may be removed or altered based on the availability and relevance of data.
Scope
Summary
Global Markets Direct's latest Pharmaceutical and Healthcare disease pipeline guide Duchenne Muscular Dystrophy - Drugs In Development, 2022, provides an overview of the Duchenne Muscular Dystrophy (Genetic Disorders) pipeline landscape.
Duchenne muscular dystrophy (DMD) is a genetic disorder that causes muscles to gradually weaken over time. Signs and symptoms of DMD include fatigue, learning difficulties, intellectual disability, muscle weakness and progressive difficulty walking. Risk factors include gender and family history. Treatment includes steroid medication, respiratory therapy and surgery.
Report Highlights
Global Markets Direct's Pharmaceutical and Healthcare latest pipeline guide Duchenne Muscular Dystrophy - Drugs In Development, 2022, provides comprehensive information on the therapeutics under development for Duchenne Muscular Dystrophy (Genetic Disorders), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.
The Duchenne Muscular Dystrophy (Genetic Disorders) pipeline guide also reviews of key players involved in therapeutic development for Duchenne Muscular Dystrophy and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Pre-Registration, Filing rejected/Withdrawn, Phase III, Phase II, Phase I, IND/CTA Filed, Preclinical, Discovery and Unknown stages are 1, 1, 7, 12, 15, 2, 71, 34 and 1 respectively. Similarly, the Universities portfolio in Phase III, Phase II, Phase I, IND/CTA Filed, Preclinical and Discovery stages comprises 2, 1, 2, 1, 13 and 3 molecules, respectively.
Duchenne Muscular Dystrophy (Genetic Disorders) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from Global Markets Direct’s proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.
Note: Certain content / sections in the pipeline guide may be removed or altered based on the availability and relevance of data.
Scope
- The pipeline guide provides a snapshot of the global therapeutic landscape of Duchenne Muscular Dystrophy (Genetic Disorders).
- The pipeline guide reviews pipeline therapeutics for Duchenne Muscular Dystrophy (Genetic Disorders) by companies and universities/research institutes based on information derived from company and industry-specific sources.
- The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.
- The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.
- The pipeline guide reviews key companies involved in Duchenne Muscular Dystrophy (Genetic Disorders) therapeutics and enlists all their major and minor projects.
- The pipeline guide evaluates Duchenne Muscular Dystrophy (Genetic Disorders) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA) and molecule type.
- The pipeline guide encapsulates all the dormant and discontinued pipeline projects.
- The pipeline guide reviews latest news related to pipeline therapeutics for Duchenne Muscular Dystrophy (Genetic Disorders)
- Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.
- Recognize emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage.
- Find and recognize significant and varied types of therapeutics under development for Duchenne Muscular Dystrophy (Genetic Disorders).
- Classify potential new clients or partners in the target demographic.
- Develop tactical initiatives by understanding the focus areas of leading companies.
- Plan mergers and acquisitions meritoriously by identifying key players and it’s most promising pipeline therapeutics.
- Formulate corrective measures for pipeline projects by understanding Duchenne Muscular Dystrophy (Genetic Disorders) pipeline depth and focus of Indication therapeutics.
- Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.
- Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from pipeline.
Table of Contents
343 Pages
- Introduction
- Global Markets Direct Report Coverage
- Duchenne Muscular Dystrophy – Overview
- Duchenne Muscular Dystrophy – Therapeutics Development
- Pipeline Overview
- Pipeline by Companies
- Pipeline by Universities/Institutes
- Products under Development by Companies
- Products under Development by Universities/Institutes
- Duchenne Muscular Dystrophy – Therapeutics Assessment
- Assessment by Target
- Assessment by Mechanism of Action
- Assessment by Route of Administration
- Assessment by Molecule Type
- Duchenne Muscular Dystrophy – Companies Involved in Therapeutics Development
- AAVogen Inc
- Alpha Anomeric
- American CryoStem Corp
- Anagenesis Biotechnologies SAS
- Antisense Therapeutics Ltd
- ARMGO Pharma Inc
- Astria Therapeutics Inc
- AUM LifeTech Inc
- Autotac Bio Inc
- Avidity Biosciences Inc
- Axolo Pharma Inc
- Bayer AG
- Biogen Inc
- BioIncept LLC
- Bioleaders Corp
- BioMarin Pharmaceutical Inc
- Biophytis SA
- CANbridge Life Sciences Ltd
- Capricor Therapeutics Inc
- Chengdu Fanxi Biopharma Co Ltd
- Code Biotherapeutics Inc
- Consortium.AI
- Constant Therapeutics LLC
- CRISPR Therapeutics AG
- Cumberland Pharmaceuticals Inc
- Daiichi Sankyo Co Ltd
- DepYmed Inc
- DMD Therapeutics Inc
- DTx Pharma Inc
- Dyne Therapeutics Inc
- Dystrogen Therapeutics SA
- Edgewise Therapeutics Inc
- Editas Medicine Inc
- Eli Lilly and Co
- Eloxx Pharmaceuticals Inc
- Encell Co Ltd
- Entrada Therapeutics Inc
- Epirium Bio Inc
- EryDel SpA
- Evox Therapeutics Ltd
- FibroGen Inc
- FibroGenesis LLC
- Fulcrum Therapeutics Inc
- InnoBioscience LLC
- Italfarmaco SpA
- Ixchel Pharma LLC
- J2H Biotech
- Keros Therapeutics Inc
- KSbitugen Co Ltd
- LambdaGen Therapeutics
- Ludi Therapeutics
- Milo Biotechnology LLC
- Mitobridge Inc
- Mitochon Pharmaceuticals Inc
- MitoRx Therapeutics Ltd
- MyoGene Bio LLC
- Myos Inc
- Myosana Therapeutics Inc
- MyoTherix Inc
- Nippon Shinyaku Co Ltd
- NS Pharma Inc
- OliPass Corporation
- OMEICOS Therapeutics GmbH
- Oncocross Co Ltd
- Oncotelic Inc
- Pepgen Ltd
- PeptiDream Inc
- Pfizer Inc
- Pharmaxis Ltd
- PhaseBio Pharmaceuticals Inc
- Pliant Therapeutics Inc
- Progenitor Therapeutics Ltd
- Prothelia Inc
- PTC Therapeutics Inc
- PYC Therapeutics Ltd
- RASRx LLC
- RegenxBio Inc
- ReoStem LLC
- Ridgeline Therapeutics LLC
- Santhera Pharmaceuticals Holding AG
- Sarcomed AB
- Sarepta Therapeutics Inc
- Satellos Bioscience Inc
- Solid Biosciences Inc
- Stealth BioTherapeutics Corp
- SteroTherapeutics LLC
- Sutura Therapeutics Ltd
- Suzhou GenAssist Therapeutics Co Ltd
- Taiho Pharmaceutical Co Ltd
- Tivorsan Pharmaceuticals Inc
- Tolerion Inc
- Triplex Therapeutics Inc
- UGISense AG
- Ultragenyx Pharmaceutical Inc
- Vandria SA
- Vertex Pharmaceuticals Inc
- Vita Therapeutics Inc
- Wave Life Sciences Ltd
- Zata Pharmaceuticals Inc
- Duchenne Muscular Dystrophy – Drug Profiles
- Anti-integrin mAb – Drug Profile
- Product Description
- Mechanism Of Action
- Antisense Oligonucleotide 1 to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Antisense Oligonucleotide for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- -Antisense Oligonucleotide to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Antisense Oligonucleotide to Inhibit TGFB2 for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- Antisense Oligonucleotides for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- Antisense Oligonucleotides to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- Antisense RNAi Oligonucleotides for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- AOC-1044 – Drug Profile
- Product Description
- Mechanism Of Action
- AP-39 – Drug Profile
- Product Description
- Mechanism Of Action
- ARM-210 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- ataluren – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- ATC-401 – Drug Profile
- Product Description
- Mechanism Of Action
- ATCell – Drug Profile
- Product Description
- Mechanism Of Action
- ATL-1102 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- AVGN-7 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- BIIB-100 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- BIO-101 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- BLSM-22 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- BMN-351 – Drug Profile
- Product Description
- Mechanism Of Action
- bocidelpar sulfate – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- CAP-1002 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- CAP-2003 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- CAT-1041 – Drug Profile
- Product Description
- Mechanism Of Action
- Cell Therapy for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- CRISPR-Based Gene Therapy for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- CYMD-201 – Drug Profile
- Product Description
- Mechanism Of Action
- delandistrogene moxeparvovec – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- dexamethasone sodium phosphate – Drug Profile
- Product Description
- Mechanism Of Action
- dextro epicatechin – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- DMD-813 – Drug Profile
- Product Description
- Mechanism Of Action
- Drug for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- DS-5144 – Drug Profile
- Product Description
- Mechanism Of Action
- DS-5150 – Drug Profile
- Product Description
- Mechanism Of Action
- DS-5151 – Drug Profile
- Product Description
- Mechanism Of Action
- DS-5153 – Drug Profile
- Product Description
- Mechanism Of Action
- DTDEC-01 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- EDG-5506 – Drug Profile
- Product Description
- Mechanism Of Action
- EDG-6289 – Drug Profile
- Product Description
- Mechanism Of Action
- elamipretide hydrochloride – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- ELX-02 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- EN-001 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- ENTR-60144 – Drug Profile
- Product Description
- Mechanism Of Action
- epicatechin – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- eteplirsen – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- finerenone – Drug Profile
- Product Description
- Mechanism Of Action
- FNX-018 – Drug Profile
- Product Description
- Mechanism Of Action
- FORCEM-23D – Drug Profile
- Product Description
- Mechanism Of Action
- fordadistrogene movaparvovec – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Fusion Protein to Activate Utrophin for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- GEN-6045 – Drug Profile
- Product Description
- Mechanism Of Action
- GEN-6050 – Drug Profile
- Product Description
- Mechanism Of Action
- GEN-6051 – Drug Profile
- Product Description
- Mechanism Of Action
- Gene Therapies to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- Gene Therapy 1 for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Gene Therapy 1 to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Gene therapy for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- Gene Therapy to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Gene therapy To Activate Follistatin For Duchenne Muscular Dystrophy, Facioscapulohumeral Muscular Dystrophy, Becker Muscular Dystrophy And Inclusion Body Myositis – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Gene Therapy to Activate GALGT2 for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Gene Therapy to Activate Utrophin for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- givinostat – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- GNT-0004 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- golodirsen – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- IB-DMD – Drug Profile
- Product Description
- Mechanism Of Action
- ifetroban – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- IXC-103 – Drug Profile
- Product Description
- Mechanism Of Action
- IXC-109 – Drug Profile
- Product Description
- Mechanism Of Action
- J-2H1803 – Drug Profile
- Product Description
- Mechanism Of Action
- JAR-914 – Drug Profile
- Product Description
- Mechanism Of Action
- KER-050 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Kinase Derivatives – Drug Profile
- Product Description
- Mechanism Of Action
- KSB-10201 – Drug Profile
- Product Description
- Mechanism Of Action
- L-citrulline + metformin – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- MA-0204 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- MG-53 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- MP-101 – Drug Profile
- Product Description
- Mechanism Of Action
- MT-002 – Drug Profile
- Product Description
- Mechanism Of Action
- Muscle Program – Drug Profile
- Product Description
- Mechanism Of Action
- Myostatin antagonist – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- nandrolone decanoate – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Next AOC DMD Programs-Exon 45 Dystrophin – Drug Profile
- Product Description
- Mechanism Of Action
- Next AOC DMD Programs-Exon 51 Dystrophin – Drug Profile
- Product Description
- Mechanism Of Action
- NS-045 – Drug Profile
- Product Description
- Mechanism Of Action
- NS-050 – Drug Profile
- Product Description
- Mechanism Of Action
- NS-051 – Drug Profile
- Product Description
- Mechanism Of Action
- NS-055 – Drug Profile
- Product Description
- Mechanism Of Action
- NS-089 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- OC-514 – Drug Profile
- Product Description
- Mechanism Of Action
- Oligonucleotide for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- Oligonucleotide to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- OMT-28 – Drug Profile
- Product Description
- Mechanism Of Action
- pamrevlumab – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- PB-1023 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- PBGENE-DMD – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- PGN-EDO45 – Drug Profile
- Product Description
- Mechanism Of Action
- PGNEDO-44 – Drug Profile
- Product Description
- Mechanism Of Action
- PGNEDO-51 – Drug Profile
- Product Description
- Mechanism Of Action
- pizuglanstat – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Preimplantation Factor – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Protein for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Protein to Target Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- PXS-4699 – Drug Profile
- Product Description
- Mechanism Of Action
- RASRx-1902 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Recombinant Protein for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- renadirsen – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- RGX-202 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- RHLAM-111 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- rimeporide – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- RTC-13 – Drug Profile
- Product Description
- Mechanism Of Action
- RTL-72484 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- SGT-001 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- SGT-003 – Drug Profile
- Product Description
- Mechanism Of Action
- Small Molecule for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- Small Molecule to Activate UTRN for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- Small Molecule to Target Androgen Receptor and Glucocorticoid Receptor for Oncology, Autoimmune diseases and Inflammatory Disorders – Drug Profile
- Product Description
- Mechanism Of Action
- Small Molecules for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- Small Molecules to Activate Utrophin for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- Small Molecules to Inhibit CLK for Solid Tumors and Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- Small Molecules to Inhibit PGD2 Synthase for Asthma and Allergic Rhinitis – Drug Profile
- Product Description
- Mechanism Of Action
- SRP-4044 – Drug Profile
- Product Description
- Mechanism Of Action
- SRP-4050 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- SRP-4052 – Drug Profile
- Product Description
- Mechanism Of Action
- SRP-4055 – Drug Profile
- Product Description
- Mechanism Of Action
- SRP-5044 – Drug Profile
- Product Description
- Mechanism Of Action
- SRP-5045 – Drug Profile
- Product Description
- Mechanism Of Action
- SRP-5050 – Drug Profile
- Product Description
- Mechanism Of Action
- SRP-5051 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- SRP-5052 – Drug Profile
- Product Description
- Mechanism Of Action
- SRP-5053 – Drug Profile
- Product Description
- Mechanism Of Action
- ST-002 – Drug Profile
- Product Description
- Mechanism Of Action
- Stem Cell Therapy 1 to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Stem Cell Therapy 2 to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Stem Cell Therapy for Amyotrophic Lateral Sclerosis and Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Stem Cell Therapy for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Stem Cell Therapy to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
- Product Description
- Mechanism Of Action
- SUT-001 – Drug Profile
- Product Description
- Mechanism Of Action
- tamoxifen citrate – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- testosterone – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- trodusquemine – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- TVN-102 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- TXA-127 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- Undisclosed-Duchenne Syndrome – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- UX-810 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- vamorolone – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- viltolarsen – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- VTA-100 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- WVEN-531 – Drug Profile
- Product Description
- Mechanism Of Action
- History of Events
- X-0112 – Drug Profile
- Product Description
- Mechanism Of Action
- Duchenne Muscular Dystrophy – Dormant Projects
- Duchenne Muscular Dystrophy – Discontinued Products
- Duchenne Muscular Dystrophy – Product Development Milestones
- Featured News & Press Releases
- Apr 28, 2022: Pfizer to open first U.S. sites in phase 3 trial of investigational gene therapy for ambulatory patients with Duchenne muscular dystrophy
- Apr 07, 2022: Dystrogen Therapeutics investigational chimeric cell therapy DT-DEC01 for the treatment of Duchene Muscular Dystrophy shows safety and functional improvements
- Apr 06, 2022: PepGen announces first participant dosed in a phase 1 clinical trial of PGN-EDO51 for the treatment of Duchenne Muscular Dystrophy
- Mar 29, 2022: Santhera and ReveraGen start rolling NDA submission to the FDA for Vamorolone for the treatment of Duchenne Muscular Dystrophy
- Mar 18, 2022: Exon 44-targeted DMD drug hits goals in PI/II: NCNP/Nippon Shinyaku
- Mar 17, 2022: The result of an investigator-initiated clinical trial (First In Human trial) of NS-089/NCNP-02 for the treatment of Duchenne muscular dystrophy
- Mar 16, 2022: Stealth BioTherapeutics showcases new Duchenne muscular dystrophy nonclinical data at the 2022 Muscular Dystrophy Association and Clinical Scientific Conference
- Mar 15, 2022: PepGen announces approval by Health Canada of CTA to begin first in human trials of PGN-EDO51 to treat Duchenne Muscular Dystrophy
- Mar 15, 2022: Santhera and ReveraGen to present efficacy and safety data with vamorolone at 2022 Muscular Dystrophy Association Conference
- Mar 14, 2022: Significant modulation of two bone morphogenetic proteins supports potential of ATL1102 for improving bone density in DMD
- Mar 11, 2022: The Lancet publishes positive results from Capricor Therapeutics’ phase 2 study evaluating CAP-1002 in late-stage Duchenne muscular dystrophy
- Mar 11, 2022: The result of an investigator-initiated clinical trial (First In Human trial) of NS-089/NCNP-02 for the treatment of Duchenne muscular dystrophy
- Mar 09, 2022: Antisense Therapeutics to present poster at world’s largest NMD conference
- Mar 08, 2022: Edgewise Therapeutics to present on EDG-5506 for Becker and Duchenne Muscular Dystrophy (BMD, DMD) at the 2022 Annual MDA Clinical and Scientific Conference
- Mar 08, 2022: Roche to present new SRP-9001 data at MDA 2022 and highlight expanding neuromuscular disease portfolio
- Appendix
- Methodology
- Coverage
- Secondary Research
- Primary Research
- Expert Panel Validation
- Contact Us
- Disclaimer
- List of Tables
- Table 1: Number of Products under Development for Duchenne Muscular Dystrophy, 2022
- Table 2: Number of Products under Development by Companies, 2022
- Table 3: Number of Products under Development by Companies, 2022 (Contd..1)
- Table 4: Number of Products under Development by Companies, 2022 (Contd..2)
- Table 5: Number of Products under Development by Companies, 2022 (Contd..3)
- Table 6: Number of Products under Development by Companies, 2022 (Contd..4)
- Table 7: Number of Products under Development by Universities/Institutes, 2022
- Table 8: Products under Development by Companies, 2022
- Table 9: Products under Development by Companies, 2022 (Contd..1)
- Table 10: Products under Development by Companies, 2022 (Contd..2)
- Table 11: Products under Development by Companies, 2022 (Contd..3)
- Table 12: Products under Development by Companies, 2022 (Contd..4)
- Table 13: Products under Development by Companies, 2022 (Contd..5)
- Table 14: Products under Development by Companies, 2022 (Contd..6)
- Table 15: Products under Development by Companies, 2022 (Contd..7)
- Table 16: Products under Development by Companies, 2022 (Contd..8)
- Table 17: Products under Development by Universities/Institutes, 2022
- Table 18: Number of Products by Stage and Target, 2022
- Table 19: Number of Products by Stage and Target, 2022 (Contd..1)
- Table 20: Number of Products by Stage and Mechanism of Action, 2022
- Table 21: Number of Products by Stage and Mechanism of Action, 2022 (Contd..1)
- Table 22: Number of Products by Stage and Route of Administration, 2022
- Table 23: Number of Products by Stage and Molecule Type, 2022
- Table 24: Duchenne Muscular Dystrophy – Pipeline by AAVogen Inc, 2022
- Table 25: Duchenne Muscular Dystrophy – Pipeline by Alpha Anomeric, 2022
- Table 26: Duchenne Muscular Dystrophy – Pipeline by American CryoStem Corp, 2022
- Table 27: Duchenne Muscular Dystrophy – Pipeline by Anagenesis Biotechnologies SAS, 2022
- Table 28: Duchenne Muscular Dystrophy – Pipeline by Antisense Therapeutics Ltd, 2022
- Table 29: Duchenne Muscular Dystrophy – Pipeline by ARMGO Pharma Inc, 2022
- Table 30: Duchenne Muscular Dystrophy – Pipeline by Astria Therapeutics Inc, 2022
- Table 31: Duchenne Muscular Dystrophy – Pipeline by AUM LifeTech Inc, 2022
- Table 32: Duchenne Muscular Dystrophy – Pipeline by Autotac Bio Inc, 2022
- Table 33: Duchenne Muscular Dystrophy – Pipeline by Avidity Biosciences Inc, 2022
- Table 34: Duchenne Muscular Dystrophy – Pipeline by Axolo Pharma Inc, 2022
- Table 35: Duchenne Muscular Dystrophy – Pipeline by Bayer AG, 2022
- Table 36: Duchenne Muscular Dystrophy – Pipeline by Biogen Inc, 2022
- Table 37: Duchenne Muscular Dystrophy – Pipeline by BioIncept LLC, 2022
- Table 38: Duchenne Muscular Dystrophy – Pipeline by Bioleaders Corp, 2022
- Table 39: Duchenne Muscular Dystrophy – Pipeline by BioMarin Pharmaceutical Inc, 2022
- Table 40: Duchenne Muscular Dystrophy – Pipeline by Biophytis SA, 2022
- Table 41: Duchenne Muscular Dystrophy – Pipeline by CANbridge Life Sciences Ltd, 2022
- Table 42: Duchenne Muscular Dystrophy – Pipeline by Capricor Therapeutics Inc, 2022
- Table 43: Duchenne Muscular Dystrophy – Pipeline by Chengdu Fanxi Biopharma Co Ltd, 2022
- Table 44: Duchenne Muscular Dystrophy – Pipeline by Code Biotherapeutics Inc, 2022
- Table 45: Duchenne Muscular Dystrophy – Pipeline by Consortium.AI, 2022
- Table 46: Duchenne Muscular Dystrophy – Pipeline by Constant Therapeutics LLC, 2022
- Table 47: Duchenne Muscular Dystrophy – Pipeline by CRISPR Therapeutics AG, 2022
- Table 48: Duchenne Muscular Dystrophy – Pipeline by Cumberland Pharmaceuticals Inc, 2022
- Table 49: Duchenne Muscular Dystrophy – Pipeline by Daiichi Sankyo Co Ltd, 2022
- Table 50: Duchenne Muscular Dystrophy – Pipeline by DepYmed Inc, 2022
- Table 51: Duchenne Muscular Dystrophy – Pipeline by DMD Therapeutics Inc, 2022
- Table 52: Duchenne Muscular Dystrophy – Pipeline by DTx Pharma Inc, 2022
- Table 53: Duchenne Muscular Dystrophy – Pipeline by Dyne Therapeutics Inc, 2022
- Table 54: Duchenne Muscular Dystrophy – Pipeline by Dystrogen Therapeutics SA, 2022
- Table 55: Duchenne Muscular Dystrophy – Pipeline by Edgewise Therapeutics Inc, 2022
- Table 56: Duchenne Muscular Dystrophy – Pipeline by Editas Medicine Inc, 2022
- Table 57: Duchenne Muscular Dystrophy – Pipeline by Eli Lilly and Co, 2022
- Table 58: Duchenne Muscular Dystrophy – Pipeline by Eloxx Pharmaceuticals Inc, 2022
- Table 59: Duchenne Muscular Dystrophy – Pipeline by Encell Co Ltd, 2022
- Table 60: Duchenne Muscular Dystrophy – Pipeline by Entrada Therapeutics Inc, 2022
- Table 61: Duchenne Muscular Dystrophy – Pipeline by Epirium Bio Inc, 2022
- Table 62: Duchenne Muscular Dystrophy – Pipeline by EryDel SpA, 2022
- Table 63: Duchenne Muscular Dystrophy – Pipeline by Evox Therapeutics Ltd, 2022
- Table 64: Duchenne Muscular Dystrophy – Pipeline by FibroGen Inc, 2022
- Table 65: Duchenne Muscular Dystrophy – Pipeline by FibroGenesis LLC, 2022
- Table 66: Duchenne Muscular Dystrophy – Pipeline by Fulcrum Therapeutics Inc, 2022
- Table 67: Duchenne Muscular Dystrophy – Pipeline by InnoBioscience LLC, 2022
- Table 68: Duchenne Muscular Dystrophy – Pipeline by Italfarmaco SpA, 2022
- Table 69: Duchenne Muscular Dystrophy – Pipeline by Ixchel Pharma LLC, 2022
- Table 70: Duchenne Muscular Dystrophy – Pipeline by J2H Biotech, 2022
- Table 71: Duchenne Muscular Dystrophy – Pipeline by Keros Therapeutics Inc, 2022
- Table 72: Duchenne Muscular Dystrophy – Pipeline by KSbitugen Co Ltd, 2022
- Table 73: Duchenne Muscular Dystrophy – Pipeline by LambdaGen Therapeutics, 2022
- Table 74: Duchenne Muscular Dystrophy – Pipeline by Ludi Therapeutics, 2022
- Table 75: Duchenne Muscular Dystrophy – Pipeline by Milo Biotechnology LLC, 2022
- Table 76: Duchenne Muscular Dystrophy – Pipeline by Mitobridge Inc, 2022
- Table 77: Duchenne Muscular Dystrophy – Pipeline by Mitochon Pharmaceuticals Inc, 2022
- Table 78: Duchenne Muscular Dystrophy – Pipeline by MitoRx Therapeutics Ltd, 2022
- Table 79: Duchenne Muscular Dystrophy – Pipeline by MyoGene Bio LLC, 2022
- Table 80: Duchenne Muscular Dystrophy – Pipeline by Myos Inc, 2022
- Table 81: Duchenne Muscular Dystrophy – Pipeline by Myosana Therapeutics Inc, 2022
- Table 82: Duchenne Muscular Dystrophy – Pipeline by MyoTherix Inc, 2022
- Table 83: Duchenne Muscular Dystrophy – Pipeline by Nippon Shinyaku Co Ltd, 2022
- Table 84: Duchenne Muscular Dystrophy – Pipeline by NS Pharma Inc, 2022
- Table 85: Duchenne Muscular Dystrophy – Pipeline by OliPass Corporation, 2022
- Table 86: Duchenne Muscular Dystrophy – Pipeline by OMEICOS Therapeutics GmbH, 2022
- Table 87: Duchenne Muscular Dystrophy – Pipeline by Oncocross Co Ltd, 2022
- Table 88: Duchenne Muscular Dystrophy – Pipeline by Oncotelic Inc, 2022
- Table 89: Duchenne Muscular Dystrophy – Pipeline by Pepgen Ltd, 2022
- Table 90: Duchenne Muscular Dystrophy – Pipeline by PeptiDream Inc, 2022
- Table 91: Duchenne Muscular Dystrophy – Pipeline by Pfizer Inc, 2022
- Table 92: Duchenne Muscular Dystrophy – Pipeline by Pharmaxis Ltd, 2022
- Table 93: Duchenne Muscular Dystrophy – Pipeline by PhaseBio Pharmaceuticals Inc, 2022
- Table 94: Duchenne Muscular Dystrophy – Pipeline by Pliant Therapeutics Inc, 2022
- Table 95: Duchenne Muscular Dystrophy – Pipeline by Progenitor Therapeutics Ltd, 2022
- Table 96: Duchenne Muscular Dystrophy – Pipeline by Prothelia Inc, 2022
- Table 97: Duchenne Muscular Dystrophy – Pipeline by PTC Therapeutics Inc, 2022
- Table 98: Duchenne Muscular Dystrophy – Pipeline by PYC Therapeutics Ltd, 2022
- Table 99: Duchenne Muscular Dystrophy – Pipeline by RASRx LLC, 2022
- Table 100: Duchenne Muscular Dystrophy – Pipeline by RegenxBio Inc, 2022
- Table 101: Duchenne Muscular Dystrophy – Pipeline by ReoStem LLC, 2022
- Table 102: Duchenne Muscular Dystrophy – Pipeline by Ridgeline Therapeutics LLC, 2022
- Table 103: Duchenne Muscular Dystrophy – Pipeline by Santhera Pharmaceuticals Holding AG, 2022
- Table 104: Duchenne Muscular Dystrophy – Pipeline by Sarcomed AB, 2022
- Table 105: Duchenne Muscular Dystrophy – Pipeline by Sarepta Therapeutics Inc, 2022
- Table 106: Duchenne Muscular Dystrophy – Pipeline by Satellos Bioscience Inc, 2022
- Table 107: Duchenne Muscular Dystrophy – Pipeline by Solid Biosciences Inc, 2022
- Table 108: Duchenne Muscular Dystrophy – Pipeline by Stealth BioTherapeutics Corp, 2022
- Table 109: Duchenne Muscular Dystrophy – P
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