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Pompe Disease Market by Therapy Type (Enzyme, Substrate), Molecule Type (Biologics, Small Molecules), Dosage Form, Route of Administration - Global Forecast 2024-2030

Publisher 360iResearch
Published Jan 15, 2024
Length 192 Pages
SKU # IRE18449170

Description

Pompe Disease Market by Therapy Type (Enzyme, Substrate), Molecule Type (Biologics, Small Molecules), Dosage Form, Route of Administration - Global Forecast 2024-2030


The Pompe Disease Market size was estimated at USD 1.50 billion in 2023 and expected to reach USD 1.59 billion in 2024, at a CAGR 5.61% to reach USD 2.21 billion by 2030.

Global Pompe Disease Market

FPNV Positioning Matrix

The FPNV Positioning Matrix is pivotal in evaluating the Pompe Disease Market. It offers a comprehensive assessment of vendors, examining key metrics related to Business Strategy and Product Satisfaction. This in-depth analysis empowers users to make well-informed decisions aligned with their requirements. Based on the evaluation, the vendors are then categorized into four distinct quadrants representing varying levels of success: Forefront (F), Pathfinder (P), Niche (N), or Vital (V).

Market Share Analysis

The Market Share Analysis is a comprehensive tool that provides an insightful and in-depth examination of the current state of vendors in the Pompe Disease Market. By meticulously comparing and analyzing vendor contributions in terms of overall revenue, customer base, and other key metrics, we can offer companies a greater understanding of their performance and the challenges they face when competing for market share. Additionally, this analysis provides valuable insights into the competitive nature of the sector, including factors such as accumulation, fragmentation dominance, and amalgamation traits observed over the base year period studied. With this expanded level of detail, vendors can make more informed decisions and devise effective strategies to gain a competitive edge in the market.

Key Company Profiles

The report delves into recent significant developments in the Pompe Disease Market, highlighting leading vendors and their innovative profiles. These include Astellas Pharma Europe Ltd, B Braun Melsungen AG, Becton, Dickinson & Company, CENTOGENE N.V., Flowserve Corporation, Genethon, GlaxoSmithKline PLC, Koninklijke Philips NV, Merck KGaA, Novartis AG, Oxyrane UK Ltd., Pfizer Inc., Pharming Group NV, Sanofi S.A., and Takeda Pharmaceutical Company Limited.

Market Segmentation & Coverage

This research report categorizes the Pompe Disease Market to forecast the revenues and analyze trends in each of the following sub-markets:

Therapy Type
Enzyme
Substrate
Molecule Type
Biologics
Small Molecules
Dosage Form
Liquid
Solid
Route of Administration
Oral
Parental
Region
Americas
Argentina
Brazil
Canada
Mexico
United States
California
Florida
Illinois
New York
Ohio
Pennsylvania
Texas
Asia-Pacific
Australia
China
India
Indonesia
Japan
Malaysia
Philippines
Singapore
South Korea
Taiwan
Thailand
Vietnam
Europe, Middle East & Africa
Denmark
Egypt
Finland
France
Germany
Israel
Italy
Netherlands
Nigeria
Norway
Poland
Qatar
Russia
Saudi Arabia
South Africa
Spain
Sweden
Switzerland
Turkey
United Arab Emirates
United Kingdom

The report offers valuable insights on the following aspects:

1. Market Penetration: It presents comprehensive information on the market provided by key players.
2. Market Development: It delves deep into lucrative emerging markets and analyzes the penetration across mature market segments.
3. Market Diversification: It provides detailed information on new product launches, untapped geographic regions, recent developments, and investments.
4. Competitive Assessment & Intelligence: It conducts an exhaustive assessment of market shares, strategies, products, certifications, regulatory approvals, patent landscape, and manufacturing capabilities of the leading players.
5. Product Development & Innovation: It offers intelligent insights on future technologies, R&D activities, and breakthrough product developments.

The report addresses key questions such as:

1. What is the market size and forecast of the Pompe Disease Market?
2. Which products, segments, applications, and areas should one consider investing in over the forecast period in the Pompe Disease Market?
3. What are the technology trends and regulatory frameworks in the Pompe Disease Market?
4. What is the market share of the leading vendors in the Pompe Disease Market?
5. Which modes and strategic moves are suitable for entering the Pompe Disease Market?

Note: PDF & Excel + Online Access - 1 Year

Table of Contents

192 Pages
1. Preface
1.1. Objectives of the Study
1.2. Market Segmentation & Coverage
1.3. Years Considered for the Study
1.4. Currency & Pricing
1.5. Language
1.6. Limitations
1.7. Assumptions
1.8. Stakeholders
2. Research Methodology
2.1. Define: Research Objective
2.2. Determine: Research Design
2.3. Prepare: Research Instrument
2.4. Collect: Data Source
2.5. Analyze: Data Interpretation
2.6. Formulate: Data Verification
2.7. Publish: Research Report
2.8. Repeat: Report Update
3. Executive Summary
4. Market Overview
4.1. Introduction
4.2. Pompe Disease Market, by Region
5. Market Insights
5.1. Market Dynamics
5.1.1. Drivers
5.1.1.1. Growing prevalence of pompe disease
5.1.1.2. Uptake of long term therapies and advancement in the diagnosis and treatment
5.1.1.3. Increasing developments in the gene therapy and enzyme replacement therapies
5.1.2. Restraints
5.1.2.1. High treatment costs of pompe diseases
5.1.3. Opportunities
5.1.3.1. Increasing investment in the research and development
5.1.3.2. Government initiatives for the development and manufacture of innovative products
5.1.4. Challenges
5.1.4.1. Lack of awareness about the treatment
5.2. Market Segmentation Analysis
5.3. Market Trend Analysis
5.4. Cumulative Impact of High Inflation
5.5. Porter’s Five Forces Analysis
5.5.1. Threat of New Entrants
5.5.2. Threat of Substitutes
5.5.3. Bargaining Power of Customers
5.5.4. Bargaining Power of Suppliers
5.5.5. Industry Rivalry
5.6. Value Chain & Critical Path Analysis
5.7. Regulatory Framework
6. Pompe Disease Market, by Therapy Type
6.1. Introduction
6.2. Enzyme
6.3. Substrate
7. Pompe Disease Market, by Molecule Type
7.1. Introduction
7.2. Biologics
7.3. Small Molecules
8. Pompe Disease Market, by Dosage Form
8.1. Introduction
8.2. Liquid
8.3. Solid
9. Pompe Disease Market, by Route of Administration
9.1. Introduction
9.2. Oral
9.3. Parental
10. Americas Pompe Disease Market
10.1. Introduction
10.2. Argentina
10.3. Brazil
10.4. Canada
10.5. Mexico
10.6. United States
11. Asia-Pacific Pompe Disease Market
11.1. Introduction
11.2. Australia
11.3. China
11.4. India
11.5. Indonesia
11.6. Japan
11.7. Malaysia
11.8. Philippines
11.9. Singapore
11.10. South Korea
11.11. Taiwan
11.12. Thailand
11.13. Vietnam
12. Europe, Middle East & Africa Pompe Disease Market
12.1. Introduction
12.2. Denmark
12.3. Egypt
12.4. Finland
12.5. France
12.6. Germany
12.7. Israel
12.8. Italy
12.9. Netherlands
12.10. Nigeria
12.11. Norway
12.12. Poland
12.13. Qatar
12.14. Russia
12.15. Saudi Arabia
12.16. South Africa
12.17. Spain
12.18. Sweden
12.19. Switzerland
12.20. Turkey
12.21. United Arab Emirates
12.22. United Kingdom
13. Competitive Landscape
13.1. FPNV Positioning Matrix
13.2. Market Share Analysis, By Key Player
13.3. Competitive Scenario Analysis, By Key Player
14. Competitive Portfolio
14.1. Key Company Profiles
14.1.1. Astellas Pharma Europe Ltd
14.1.2. B Braun Melsungen AG
14.1.3. Becton, Dickinson & Company
14.1.4. CENTOGENE N.V.
14.1.5. Flowserve Corporation
14.1.6. Genethon
14.1.7. GlaxoSmithKline PLC
14.1.8. Koninklijke Philips NV
14.1.9. Merck KGaA
14.1.10. Novartis AG
14.1.11. Oxyrane UK Ltd.
14.1.12. Pfizer Inc.
14.1.13. Pharming Group NV
14.1.14. Sanofi S.A.
14.1.15. Takeda Pharmaceutical Company Limited
14.2. Key Product Portfolio
15. Appendix
15.1. Discussion Guide
15.2. License & Pricing
FIGURE 1. POMPE DISEASE MARKET RESEARCH PROCESS
FIGURE 2. POMPE DISEASE MARKET SIZE, 2023 VS 2030
FIGURE 3. POMPE DISEASE MARKET SIZE, 2018-2030 (USD MILLION)
FIGURE 4. POMPE DISEASE MARKET SIZE, BY REGION, 2023 VS 2030 (%)
FIGURE 5. POMPE DISEASE MARKET SIZE, BY REGION, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 6. POMPE DISEASE MARKET DYNAMICS
FIGURE 7. POMPE DISEASE MARKET SIZE, BY THERAPY TYPE, 2023 VS 2030 (%)
FIGURE 8. POMPE DISEASE MARKET SIZE, BY THERAPY TYPE, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 9. POMPE DISEASE MARKET SIZE, BY MOLECULE TYPE, 2023 VS 2030 (%)
FIGURE 10. POMPE DISEASE MARKET SIZE, BY MOLECULE TYPE, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 11. POMPE DISEASE MARKET SIZE, BY DOSAGE FORM, 2023 VS 2030 (%)
FIGURE 12. POMPE DISEASE MARKET SIZE, BY DOSAGE FORM, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 13. POMPE DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2023 VS 2030 (%)
FIGURE 14. POMPE DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 15. AMERICAS POMPE DISEASE MARKET SIZE, BY COUNTRY, 2023 VS 2030 (%)
FIGURE 16. AMERICAS POMPE DISEASE MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 17. UNITED STATES POMPE DISEASE MARKET SIZE, BY STATE, 2023 VS 2030 (%)
FIGURE 18. UNITED STATES POMPE DISEASE MARKET SIZE, BY STATE, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 19. ASIA-PACIFIC POMPE DISEASE MARKET SIZE, BY COUNTRY, 2023 VS 2030 (%)
FIGURE 20. ASIA-PACIFIC POMPE DISEASE MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 21. EUROPE, MIDDLE EAST & AFRICA POMPE DISEASE MARKET SIZE, BY COUNTRY, 2023 VS 2030 (%)
FIGURE 22. EUROPE, MIDDLE EAST & AFRICA POMPE DISEASE MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 23. POMPE DISEASE MARKET, FPNV POSITIONING MATRIX, 2023
FIGURE 24. POMPE DISEASE MARKET SHARE, BY KEY PLAYER, 2023

Pricing

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