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Phenylketonuria (PKU) Treatment Market, Opportunity, Growth Drivers, Industry Trend Analysis and Forecast, 2024-2032

Publisher Global Market Insights
Published Aug 27, 2024
Length 223 Pages
SKU # GMI19204976

Description

Phenylketonuria (PKU) Treatment Market, Opportunity, Growth Drivers, Industry Trend Analysis and Forecast, 2024-2032


The global phenylketonuria (PKU) treatment market was valued at USD 737.7 million in 2023 and is projected to expand at a CAGR of 7.2% from 2024 to 2032. The rising demand for PKU treatments is driven by a global increase in PKU cases and advancements in treatment methods.

Enhanced newborn screening initiatives facilitate earlier PKU detections, boosting the demand for effective management therapies. Concurrently, active research and development are producing innovative therapeutic options, including gene therapy and novel drug formulations, which promise improved patient outcomes. For instance, in November 2023, the Perelman School of Medicine at the University of Pennsylvania unveiled research on future treatments using advanced CRISPR gene editing techniques, specifically prime and base editing. These advancements are poised to introduce groundbreaking therapies in genetic medicine. Moreover, increased awareness among healthcare professionals and patients about the benefits of timely and sustained treatment is further driving the PKU treatment market.

The overall phenylketonuria treatment market is classified based on PKU type, treatment type, age group, route of administration, end-user, and region.

Classic PKU segment is estimated to grow at a 7% CAGR through 2032. Its prevalence and the necessity for lifelong management underscore its market dominance. Stringent dietary controls and constant monitoring are essential for classic PKU patients. This form of PKU drives the demand for treatments like dietary supplements, medications, and emerging therapies. The extensive management needs and sizable patient population lead to a market focus on solutions that effectively regulate phenylalanine levels and prevent long-term complications.

In 2023, drug therapy emerged as the leading segment, capturing a market share of 54.5%. This prominence is due to drug therapy's crucial role in managing PKU, especially for patients who struggle to maintain control through dietary measures alone. Medications, including sapropterin dihydrochloride and other emerging therapies, play a vital role in lowering blood phenylalanine levels, leading to significant improvements in patient outcomes. The expanding availability of targeted drug therapies and advancements in pharmacological treatments are addressing unmet needs and increasing market demand. Furthermore, these drug therapies complement dietary management, fostering more comprehensive and adaptable treatment regimens for PKU patients.

In 2023, the U.S. phenylketonuria treatment market was valued at USD 280.6 million, with projections pointing towards USD 502.5 million by 2032. This robust growth is largely due to breakthroughs in diagnostic and therapeutic technologies. Innovations in genetic testing and specialized medical foods are revolutionizing PKU management, emphasizing early detection and personalized treatment strategies. The integration of advanced technologies, like next-generation sequencing, is refining genetic testing accuracy and enhancing dietary management products. These technological strides not only bolster treatment outcomes but also create lucrative opportunities for the market players in the U.S.

Table of Contents

223 Pages
Chapter 1 Methodology and Scope
1.1 Market scope and definitions
1.2 Research design
1.2.1 Research approach
1.2.2 Data collection methods
1.3 Base estimates and calculations
1.3.1 Base year calculation
1.3.2 Key trends for market estimation
1.4 Forecast model
1.5 Primary research and validation
1.5.1 Primary sources
1.5.2 Data mining sources
Chapter 2 Executive Summary
2.1 Industry 360° synopsis
Chapter 3 Industry Insights
3.1 Industry ecosystem analysis
3.2 Industry impact forces
3.2.1 Growth drivers
3.2.1.1 Rising prevalence of PKU
3.2.1.2 Advancements in new therapies for PKU
3.2.1.3 Enhanced newborn screening programs
3.2.1.4 Growing awareness for early screening and treatment
3.2.2 Industry pitfalls and challenges
3.2.2.1 Stringent regulatory requirements
3.3 Growth potential analysis
3.4 Reimbursement scenario
3.5 Pipeline analysis
3.6 Regulatory landscape
3.7 Porter's analysis
3.8 PESTEL analysis
Chapter 4 Competitive Landscape, 2023
4.1 Introduction
4.2 Company matrix analysis
4.3 Competitive analysis of major market players
4.4 Competitive positioning matrix
4.5 Strategy dashboard
Chapter 5 Market Estimates and Forecast, By PKU Type, 2021 – 2032 ($ Mn)
5.1 Key trends
5.2 Classic PKU
5.3 Mild PKU
5.4 Moderate or variant PKU
5.5 Hyperphenylalaninemia
Chapter 6 Market Estimates and Forecast, By Treatment Type, 2021 – 2032 ($ Mn)
6.1 Key trends
6.2 Drug therapy
6.3 Dietary management
6.4 Other treatment types
Chapter 7 Market Estimates and Forecast, By Age Group, 2021 – 2032 ($ Mn)
7.1 Key trends
7.2 Pediatrics
7.3 Adults
Chapter 8 Market Estimates and Forecast, By Route of Administration, 2021 – 2032 ($ Mn)
8.1 Key trends
8.2 Oral
8.3 Parenteral
Chapter 9 Market Estimates and Forecast, By End-user, 2021 – 2032 ($ Mn)
9.1 Key trends
9.2 Hospitals
9.3 Specialty clinics
9.4 Other end-users
Chapter 10 Market Estimates and Forecast, By Region, 2021 – 2032 ($ Mn)
10.1 Key trends
10.2 North America
10.2.1 U.S.
10.2.2 Canada
10.3 Europe
10.3.1 Germany
10.3.2 UK
10.3.3 France
10.3.4 Spain
10.3.5 Italy
10.3.6 Netherlands
10.3.7 Rest of Europe
10.4 Asia Pacific
10.4.1 China
10.4.2 Japan
10.4.3 India
10.4.4 Australia
10.4.5 South Korea
10.4.6 Rest of Asia Pacific
10.5 Latin America
10.5.1 Brazil
10.5.2 Mexico
10.5.3 Rest of Latin America
10.6 Middle East and Africa
10.6.1 South Africa
10.6.2 Saudi Arabia
10.6.3 UAE
10.6.4 Rest of Middle East and Africa
Chapter 11 Company Profiles
11.1 Abbott Laboratories
11.2 American Gene Technologies
11.3 APR Applied Pharma Research s.a.
11.4 BioMarin Pharmaceutical Inc.
11.5 Codexis, Inc.
11.6 Erytech Pharma SA
11.7 Homology Medicines, Inc.
11.8 Lysogene S.A.
11.9 PIAM Farmaceutici S.P.A.
11.10 Pluvia AS
11.11 PTC Therapeutics
11.12 SOM Innovation Biotech SL
11.13 Synlogic
11.14 Ultragenyx (Dimension Therapeutics)
11.15 Vitaflo International Ltd.

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