
Usher Syndrome - Pipeline Insight, 2024
Description
Usher Syndrome - Pipeline Insight, 2024
DelveInsight’s, “Usher Syndrome - Pipeline Insight, 2024,” report provides comprehensive insights about 5+ companies and 7+ pipeline drugs in Usher Syndrome pipeline landscape. It covers the pipeline drug profiles, including clinical and nonclinical stage products. It also covers the therapeutics assessment by product type, stage, route of administration, and molecule type. It further highlights the inactive pipeline products in this space.
Geography Covered
- Global coverage
Usher Syndrome: Overview
Usher syndrome is a rare genetic disorder characterized by a combination of hearing loss and progressive vision loss due to retinitis pigmentosa. It is the most common condition that affects both hearing and vision simultaneously. USH has been grouped into three main clinical types: 1, 2, and 3, which are caused by mutations in different genes and are further divided into different subtypes. Type 1 is marked by profound deafness at birth and early-onset vision loss, type 2 by moderate to severe hearing impairment and later-onset vision loss, and type 3 by progressive hearing loss and variable onset of vision loss.
Diagnosis of Usher Syndrome involves pertinent questions regarding the person’s medical history and testing of hearing, balance, and vision. A hearing (audiologic) exam measures the frequency and loudness of sounds that a person can hear. An electroretinogram measures the electrical response to the light-sensitive cells in the retina of the eyes. A retinal exam is done to observe the retina and other structures in the back of the eye. Vestibular (balance) function can be assessed by a variety of tests that evaluate different parts of the balance system. Genetic testing is clinically available for most of the genes associated with Usher Syndrome.
Presently, there is no cure for Usher Syndrome. Treatment involves managing hearing, vision, and balance problems. Some researchers have shown that taking a specific daily dose of vitamin A may slow the progression of retinal degeneration in some people with typical RP and Usher Syndrome type 2. Typically, treatment for hearing management includes hearing aids, assistive listening devices, cochlear implants, or other communication methods. Although some ophthalmologists believe that a high dose of vitamin A palmitate may slow, but not halt the progression of retinitis pigmentosa. Other treatments such as gene therapy, drug based therapy, artificial organ replacement are currently leading the market. Ongoing research on the Usher proteins function in auditory and visual cells will be important in determining the optimal target for gene replacement therapy.
""Usher Syndrome - Pipeline Insight, 2024"" report by DelveInsight outlays comprehensive insights of present scenario and growth prospects across the indication. A detailed picture of the Usher Syndrome pipeline landscape is provided which includes the disease overview and Usher Syndrome treatment guidelines. The assessment part of the report embraces, in depth Usher Syndrome commercial assessment and clinical assessment of the pipeline products under development. In the report, detailed description of the drug is given which includes mechanism of action of the drug, clinical studies, NDA approvals (if any), and product development activities comprising the technology, Usher Syndrome collaborations, licensing, mergers and acquisition, funding, designations and other product related details.
Report Highlights
- The companies and academics are working to assess challenges and seek opportunities that could influence Usher Syndrome R&D. The therapies under development are focused on novel approaches to treat/improve Usher Syndrome.
This segment of the Usher Syndrome report encloses its detailed analysis of various drugs in different stages of clinical development, including phase III, II, I, preclinical and Discovery. It also helps to understand clinical trial details, expressive pharmacological action, agreements and collaborations, and the latest news and press releases.
Usher Syndrome Emerging Drugs
- Ultevursen: Laboratoires Théa
Further product details are provided in the report……..
Usher Syndrome: Therapeutic Assessment
This segment of the report provides insights about the different Usher Syndrome drugs segregated based on following parameters that define the scope of the report, such as:
- Major Players in Usher Syndrome
- Phases
- Late stage products (Phase III)
- Mid-stage products (Phase II)
- Early-stage product (Phase I) along with the details of
- Pre-clinical and Discovery stage candidates
- Discontinued & Inactive candidates
- Route of Administration
- Oral
- Parenteral
- intravenous
- Subcutaneous
- Topical.
- Molecule Type
- Monoclonal Antibody
- Peptides
- Polymer
- Small molecule
- Gene therapy
- Product Type
Usher Syndrome: Pipeline Development Activities
The report provides insights into different therapeutic candidates in phase III, II, I, preclinical and discovery stage. It also analyses Usher Syndrome therapeutic drugs key players involved in developing key drugs.
Pipeline Development Activities
The report covers the detailed information of collaborations, acquisition and merger, licensing along with a thorough therapeutic assessment of emerging Usher Syndrome drugs.
Usher Syndrome Report Insights
- Usher Syndrome Pipeline Analysis
- Therapeutic Assessment
- Unmet Needs
- Impact of Drugs
- Pipeline Product Profiles
- Therapeutic Assessment
- Pipeline Assessment
- Inactive drugs assessment
- Unmet Needs
Current Treatment Scenario and Emerging Therapies:
- How many companies are developing Usher Syndrome drugs?
- How many Usher Syndrome drugs are developed by each company?
- How many emerging drugs are in mid-stage, and late-stage of development for the treatment of Usher Syndrome?
- What are the key collaborations (Industry–Industry, Industry–Academia), Mergers and acquisitions, licensing activities related to the Usher Syndrome therapeutics?
- What are the recent trends, drug types and novel technologies developed to overcome the limitation of existing therapies?
- What are the clinical studies going on for Usher Syndrome and their status?
- What are the key designations that have been granted to the emerging drugs?
- Laboratoires Théa
- Nacuity Pharmaceuticals
- Eli Lilly and Company
- Odylia Therapeutics
- AAV- USH1C
- NPI-001
- Ultevursen
- AK-CLRN1
Table of Contents
60 Pages
- Introduction
- Executive Summary
- Usher Syndrome: Overview
- Causes
- Mechanism of Action
- Signs and Symptoms
- Diagnosis
- Disease Management
- Pipeline Therapeutics
- Comparative Analysis
- Therapeutic Assessment
- Assessment by Product Type
- Assessment by Stage and Product Type
- Assessment by Route of Administration
- Assessment by Stage and Route of Administration
- Assessment by Molecule Type
- Assessment by Stage and Molecule Type
- Usher Syndrome – DelveInsight’s Analytical Perspective
- Mid Stage Products (Phase II/III)
- Comparative Analysis
- Ultevursen: Laboratoires Théa
- Product Description
- Research and Development
- Product Development Activities
- Drug profiles in the detailed report…..
- Mid Stage Products (Phase II)
- Comparative Analysis
- Drug Name: Company Name
- Product Description
- Research and Development
- Product Development Activities
- Drug profiles in the detailed report…..
- Early Stage Products (Phase I/II)
- Comparative Analysis
- NPI-001: Nacuity Pharmaceuticals
- Product Description
- Research and Development
- Product Development Activities
- Drug profiles in the detailed report…..
- Preclinical and Discovery Stage Products
- Comparative Analysis
- AAV- USH1C: Odylia Therapeutics
- Product Description
- Research and Development
- Product Development Activities
- Drug profiles in the detailed report…..
- Inactive Products
- Comparative Analysis
- Usher Syndrome Key Companies
- Usher Syndrome Key Products
- Usher Syndrome- Unmet Needs
- Usher Syndrome- Market Drivers and Barriers
- Usher Syndrome- Future Perspectives and Conclusion
- Usher Syndrome Analyst Views
- Usher Syndrome Key Companies
- Appendix
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