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Rare Hematology Global Market Report 2025

Published Oct 23, 2025
Length 250 Pages
SKU # BRC20492549

Description

Rare Hematology Global Market Report 2025 from The Business Research Company provides strategists, marketers and senior management with the critical information they need to assess the market.

This report focuses on rare hematology market which is experiencing strong growth. The report gives a guide to the trends which will be shaping the market over the next ten years and beyond.

Reasons to Purchase
  • Gain a truly global perspective with the most comprehensive report available on this market covering 15 geographies.
  • Assess the impact of key macro factors such as geopolitical conflicts, trade policies and tariffs, post-pandemic supply chain realignment, inflation and interest rate fluctuations, and evolving regulatory landscapes.
  • Create regional and country strategies on the basis of local data and analysis.
  • Identify growth segments for investment.
  • Outperform competitors using forecast data and the drivers and trends shaping the market.
  • Understand customers based on the latest market shares.
  • Benchmark performance against key competitors.
  • Suitable for supporting your internal and external presentations with reliable high quality data and analysis
  • Report will be updated with the latest data and delivered to you within 2-3 working days of order along with an Excel data sheet for easy data extraction and analysis.
  • All data from the report will also be delivered in an excel dashboard format.
Description:

Where is the largest and fastest growing market for rare hematology ? How does the market relate to the overall economy, demography and other similar markets? What forces will shape the market going forward, including technological disruption, regulatory shifts, and changing consumer preferences? The rare hematology market global report from the Business Research Company answers all these questions and many more.

The report covers market characteristics, size and growth, segmentation, regional and country breakdowns, competitive landscape, market shares, trends and strategies for this market. It traces the market’s historic and forecast market growth by geography.
  • The market characteristics section of the report defines and explains the market.
  • The market size section gives the market size ($b) covering both the historic growth of the market, and forecasting its development.
  • The forecasts are made after considering the major factors currently impacting the market. These include:
  • The forecasts are made after considering the major factors currently impacting the market. These include the technological advancements such as AI and automation, Russia-Ukraine war, trade tariffs (government-imposed import/export duties), elevated inflation and interest rates.
  • Market segmentations break down the market into sub markets.
  • The regional and country breakdowns section gives an analysis of the market in each geography and the size of the market by geography and compares their historic and forecast growth.
  • The competitive landscape chapter gives a description of the competitive nature of the market, market shares, and a description of the leading companies. Key financial deals which have shaped the market in recent years are identified.
  • The trends and strategies section analyses the shape of the market as it emerges from the crisis and suggests how companies can grow as the market recovers.
Scope

Markets Covered:1) By Disease Type: Hemophilia; Sickle Cell Disease; Thalassemia; Myelodysplastic Syndromes; Other Disease Types

2) By Treatment Type: Gene Therapy; Stem Cell Transplantation; Blood Transfusion; Pharmacotherapy

3) By Diagnostic Technique: Laboratory Tests; Blood Tests; Bone Marrow Biopsies; Imaging Techniques; Magnetic Resonance Imaging (MRI) Scans; Ultrasounds; Genetic Testing; Carrier Screening; Whole Genome Sequencing

4) By Application: Pediatric; Adult

5) By End-User: Hospitals; Specialty Clinics; Research Institutes

Subsegments:

1) By Hemophilia: Hemophilia A; Hemophilia B; Hemophilia C; Acquired Hemophilia

2) By Sickle Cell Disease: Sickle Cell Anemia; Sickle Hemoglobin C Disease; Sickle Beta Thalassemia

3) By Thalassemia: Alpha Thalassemia; Beta Thalassemia

4) By Myelodysplastic Syndromes: Refractory Anemia (RA); Refractory Anemia With Ring Sideroblasts (RARS); Refractory Cytopenia With Multilineage Dysplasia (RCMD); Refractory Anemia With Excess Blasts (RAEB); Myelodysplastic Syndrome With Isolated Del(5Q); Unclassified Myelodysplastic Syndromes

5) By Other Disease Types: Aplastic Anemia; Paroxysmal Nocturnal Hemoglobinuria; Rare Coagulation Disorders

Companies Mentioned: F. Hoffmann-La Roche Ltd; Pfizer Inc.; Abbvie Inc.; Bayer AG; Sanofi S.A.; Novartis AG; Astrazeneca Plc; Bristol-Myers Squibb Company; Takeda Pharmaceutical Company Limited; Amgen Inc.; CSL Behring LLC; Biogen Inc.; Jazz Pharmaceuticals Plc; Octapharma AG; PharmaEssentia Corporation; Disc Medicine Inc.; BioInvent International AB; Mustang Bio Inc.; BlueSphere Bio Inc.; Rallybio LLC

Countries: Australia; Brazil; China; France; Germany; India; Indonesia; Japan; Russia; South Korea; UK; USA; Canada; Italy; Spain

Regions: Asia-Pacific; Western Europe; Eastern Europe; North America; South America; Middle East; Africa

Time Series: Five years historic and ten years forecast.

Data: Ratios of market size and growth to related markets, GDP proportions, expenditure per capita,

Data Segmentations: country and regional historic and forecast data, market share of competitors, market segments.

Sourcing and Referencing: Data and analysis throughout the report is sourced using end notes.

Delivery Format: PDF, Word and Excel Data Dashboard.

Please Note: Report will be updated with the latest data and delivered to you within 3-5 working days of order.

Table of Contents

250 Pages
1. Executive Summary
2. Rare Hematology Market Characteristics
3. Rare Hematology Market Trends And Strategies
4. Rare Hematology Market - Macro Economic Scenario Including The Impact Of Interest Rates, Inflation, Geopolitics, Trade Wars and Tariffs, And Covid And Recovery On The Market
4.1. Supply Chain Impact from Tariff War & Trade Protectionism
5. Global Rare Hematology Growth Analysis And Strategic Analysis Framework
5.1. Global Rare Hematology PESTEL Analysis (Political, Social, Technological, Environmental and Legal Factors, Drivers and Restraints)
5.2. Analysis Of End Use Industries
5.3. Global Rare Hematology Market Growth Rate Analysis
5.4. Global Rare Hematology Historic Market Size and Growth, 2019 - 2024, Value ($ Billion)
5.5. Global Rare Hematology Forecast Market Size and Growth, 2024 - 2029, 2034F, Value ($ Billion)
5.6. Global Rare Hematology Total Addressable Market (TAM)
6. Rare Hematology Market Segmentation
6.1. Global Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Hemophilia
Sickle Cell Disease
Thalassemia
Myelodysplastic Syndromes
Other Disease Types
6.2. Global Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Gene Therapy
Stem Cell Transplantation
Blood Transfusion
Pharmacotherapy
6.3. Global Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Laboratory Tests
Blood Tests
Bone Marrow Biopsies
Imaging Techniques
Magnetic Resonance Imaging (MRI) Scans
Ultrasounds
Genetic Testing
Carrier Screening
Whole Genome Sequencing
6.4. Global Rare Hematology Market, Segmentation By Application, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Pediatric
Adult
6.5. Global Rare Hematology Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Hospitals
Specialty Clinics
Research Institutes
6.6. Global Rare Hematology Market, Sub-Segmentation Of Hemophilia, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Hemophilia A
Hemophilia B
Hemophilia C
Acquired Hemophilia
6.7. Global Rare Hematology Market, Sub-Segmentation Of Sickle Cell Disease, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Sickle Cell Anemia
Sickle Hemoglobin C Disease
Sickle Beta Thalassemia
6.8. Global Rare Hematology Market, Sub-Segmentation Of Thalassemia, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Alpha Thalassemia
Beta Thalassemia
6.9. Global Rare Hematology Market, Sub-Segmentation Of Myelodysplastic Syndromes, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Refractory Anemia (RA)
Refractory Anemia With Ring Sideroblasts (RARS)
Refractory Cytopenia With Multilineage Dysplasia (RCMD)
Refractory Anemia With Excess Blasts (RAEB)
Myelodysplastic Syndrome With Isolated Del(5Q)
Unclassified Myelodysplastic Syndromes
6.10. Global Rare Hematology Market, Sub-Segmentation Of Other Disease Types, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Aplastic Anemia
Paroxysmal Nocturnal Hemoglobinuria
Rare Coagulation Disorders
7. Rare Hematology Market Regional And Country Analysis
7.1. Global Rare Hematology Market, Split By Region, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
7.2. Global Rare Hematology Market, Split By Country, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
8. Asia-Pacific Rare Hematology Market
8.1. Asia-Pacific Rare Hematology Market Overview
Region Information, Market Information, Background Information, Government Initiatives, Regulations, Regulatory Bodies, Major Associations, Taxes Levied, Corporate Tax Structure, Investments, Major Companies
8.2. Asia-Pacific Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
8.3. Asia-Pacific Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
8.4. Asia-Pacific Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
9. China Rare Hematology Market
9.1. China Rare Hematology Market Overview
9.2. China Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion
9.3. China Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion
9.4. China Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion
10. India Rare Hematology Market
10.1. India Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
10.2. India Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
10.3. India Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
11. Japan Rare Hematology Market
11.1. Japan Rare Hematology Market Overview
11.2. Japan Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
11.3. Japan Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
11.4. Japan Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
12. Australia Rare Hematology Market
12.1. Australia Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
12.2. Australia Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
12.3. Australia Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
13. Indonesia Rare Hematology Market
13.1. Indonesia Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
13.2. Indonesia Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
13.3. Indonesia Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
14. South Korea Rare Hematology Market
14.1. South Korea Rare Hematology Market Overview
14.2. South Korea Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
14.3. South Korea Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
14.4. South Korea Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
15. Western Europe Rare Hematology Market
15.1. Western Europe Rare Hematology Market Overview
15.2. Western Europe Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
15.3. Western Europe Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
15.4. Western Europe Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
16. UK Rare Hematology Market
16.1. UK Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
16.2. UK Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
16.3. UK Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
17. Germany Rare Hematology Market
17.1. Germany Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
17.2. Germany Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
17.3. Germany Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
18. France Rare Hematology Market
18.1. France Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
18.2. France Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
18.3. France Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
19. Italy Rare Hematology Market
19.1. Italy Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
19.2. Italy Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
19.3. Italy Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
20. Spain Rare Hematology Market
20.1. Spain Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
20.2. Spain Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
20.3. Spain Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
21. Eastern Europe Rare Hematology Market
21.1. Eastern Europe Rare Hematology Market Overview
21.2. Eastern Europe Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
21.3. Eastern Europe Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
21.4. Eastern Europe Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
22. Russia Rare Hematology Market
22.1. Russia Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
22.2. Russia Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
22.3. Russia Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
23. North America Rare Hematology Market
23.1. North America Rare Hematology Market Overview
23.2. North America Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
23.3. North America Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
23.4. North America Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
24. USA Rare Hematology Market
24.1. USA Rare Hematology Market Overview
24.2. USA Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
24.3. USA Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
24.4. USA Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
25. Canada Rare Hematology Market
25.1. Canada Rare Hematology Market Overview
25.2. Canada Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
25.3. Canada Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
25.4. Canada Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
26. South America Rare Hematology Market
26.1. South America Rare Hematology Market Overview
26.2. South America Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
26.3. South America Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
26.4. South America Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
27. Brazil Rare Hematology Market
27.1. Brazil Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
27.2. Brazil Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
27.3. Brazil Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
28. Middle East Rare Hematology Market
28.1. Middle East Rare Hematology Market Overview
28.2. Middle East Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
28.3. Middle East Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
28.4. Middle East Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
29. Africa Rare Hematology Market
29.1. Africa Rare Hematology Market Overview
29.2. Africa Rare Hematology Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
29.3. Africa Rare Hematology Market, Segmentation By Treatment Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
29.4. Africa Rare Hematology Market, Segmentation By Diagnostic Technique, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
30. Rare Hematology Market Competitive Landscape And Company Profiles
30.1. Rare Hematology Market Competitive Landscape
30.2. Rare Hematology Market Company Profiles
30.2.1. F. Hoffmann-La Roche Ltd Overview, Products and Services, Strategy and Financial Analysis
30.2.2. Pfizer Inc. Overview, Products and Services, Strategy and Financial Analysis
30.2.3. Abbvie Inc. Overview, Products and Services, Strategy and Financial Analysis
30.2.4. Bayer AG Overview, Products and Services, Strategy and Financial Analysis
30.2.5. Sanofi S.A. Overview, Products and Services, Strategy and Financial Analysis
31. Rare Hematology Market Other Major And Innovative Companies
31.1. Novartis AG
31.2. Astrazeneca Plc
31.3. Bristol-Myers Squibb Company
31.4. Takeda Pharmaceutical Company Limited
31.5. Amgen Inc.
31.6. CSL Behring LLC
31.7. Biogen Inc.
31.8. Jazz Pharmaceuticals Plc
31.9. Octapharma AG
31.10. PharmaEssentia Corporation
31.11. Disc Medicine Inc.
31.12. BioInvent International AB
31.13. Mustang Bio Inc.
31.14. BlueSphere Bio Inc.
31.15. Rallybio LLC
32. Global Rare Hematology Market Competitive Benchmarking And Dashboard
33. Key Mergers And Acquisitions In The Rare Hematology Market
34. Recent Developments In The Rare Hematology Market
35. Rare Hematology Market High Potential Countries, Segments and Strategies
35.1 Rare Hematology Market In 2029 - Countries Offering Most New Opportunities
35.2 Rare Hematology Market In 2029 - Segments Offering Most New Opportunities
35.3 Rare Hematology Market In 2029 - Growth Strategies
35.3.1 Market Trend Based Strategies
35.3.2 Competitor Strategies
36. Appendix
36.1. Abbreviations
36.2. Currencies
36.3. Historic And Forecast Inflation Rates
36.4. Research Inquiries
36.5. The Business Research Company
36.6. Copyright And Disclaimer
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