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Niemann-Pick Disease Type C Treatment Global Market Report 2025

Published Jun 17, 2025
Length 175 Pages
SKU # BRC20111110

Description

Niemann-Pick Disease Type C Treatment Global Market Report 2025 from The Business Research Company provides strategists, marketers and senior management with the critical information they need to assess the market.

This report focuses on niemann-pick disease type c treatment market which is experiencing strong growth. The report gives a guide to the trends which will be shaping the market over the next ten years and beyond.

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Description:

Where is the largest and fastest growing market for niemann-pick disease type c treatment ? How does the market relate to the overall economy, demography and other similar markets? What forces will shape the market going forward? The niemann-pick disease type c treatment market global report from the Business Research Company answers all these questions and many more.

The report covers market characteristics, size and growth, segmentation, regional and country breakdowns, competitive landscape, market shares, trends and strategies for this market. It traces the market’s historic and forecast market growth by geography.
  • The market characteristics section of the report defines and explains the market.
  • The market size section gives the market size ($b) covering both the historic growth of the market, and forecasting its development.
  • The forecasts are made after considering the major factors currently impacting the market. These include:
  • The forecasts are made after considering the major factors currently impacting the market. These include the Russia-Ukraine war, rising inflation, higher interest rates, and the legacy of the COVID-19 pandemic.
  • Market segmentations break down the market into sub markets.
  • The regional and country breakdowns section gives an analysis of the market in each geography and the size of the market by geography and compares their historic and forecast growth. It covers the growth trajectory of COVID-19 for all regions, key developed countries and major emerging markets.
  • The competitive landscape chapter gives a description of the competitive nature of the market, market shares, and a description of the leading companies. Key financial deals which have shaped the market in recent years are identified.
  • The trends and strategies section analyses the shape of the market as it emerges from the crisis and suggests how companies can grow as the market recovers.
Scope

Markets Covered:1) By Disease Type: Niemann-Pick Diseases Type C1; Niemann-Pick Diseases Type C2

2) By Age Group: Infantile; Juvenile; Adult

3) By End-User: Hospitals; Specialty Clinics; Research And Academic Institutes

Subsegments:

1) By Niemann-Pick Disease Type C1: Pharmacological Treatment; Gene Therapy; Substrate Reduction Therapy; Supportive Care

2) By Niemann-Pick Disease Type C2: Enzyme Replacement Therapy; Pharmacological Treatment; Gene Therapy; Supportive Care

Companies Mentioned: Merck & Co. Inc.; Mayo Clinic; Boston Children's Hospital; Cincinnati Children's Hospital Medical Center; Mallinckrodt Pharmaceuticals

Countries: Australia; Brazil; China; France; Germany; India; Indonesia; Japan; Russia; South Korea; UK; USA; Canada; Italy; Spain

Regions: Asia-Pacific; Western Europe; Eastern Europe; North America; South America; Middle East; Africa

Time series: Five years historic and ten years forecast.

Data: Ratios of market size and growth to related markets, GDP proportions, expenditure per capita,

Data segmentations: country and regional historic and forecast data, market share of competitors, market segments.

Sourcing and Referencing: Data and analysis throughout the report is sourced using end notes.

Delivery Format: PDF, Word and Excel Data Dashboard.

Please Note: Report will be updated with the latest data and delivered to you within 3-5 working days of order.

Table of Contents

175 Pages
1. Executive Summary
2. Niemann-Pick Disease Type C Treatment Market Characteristics
3. Niemann-Pick Disease Type C Treatment Market Trends And Strategies
4. Niemann-Pick Disease Type C Treatment Market - Macro Economic Scenario Including The Impact Of Interest Rates, Inflation, Geopolitics, Trade Wars and Tariffs, And Covid And Recovery On The Market
5. Global Niemann-Pick Disease Type C Treatment Growth Analysis And Strategic Analysis Framework
5.1. Global Niemann-Pick Disease Type C Treatment PESTEL Analysis (Political, Social, Technological, Environmental and Legal Factors, Drivers and Restraints)
5.2. Analysis Of End Use Industries
5.3. Global Niemann-Pick Disease Type C Treatment Market Growth Rate Analysis
5.4. Global Niemann-Pick Disease Type C Treatment Historic Market Size and Growth, 2019 - 2024, Value ($ Billion)
5.5. Global Niemann-Pick Disease Type C Treatment Forecast Market Size and Growth, 2024 - 2029, 2034F, Value ($ Billion)
5.6. Global Niemann-Pick Disease Type C Treatment Total Addressable Market (TAM)
6. Niemann-Pick Disease Type C Treatment Market Segmentation
6.1. Global Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Niemann-Pick Diseases Type C1
Niemann-Pick Diseases Type C2
6.2. Global Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Infantile
Juvenile
Adult
6.3. Global Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Hospitals
Specialty Clinics
Research And Academic Institutes
6.4. Global Niemann-Pick Disease Type C Treatment Market, Sub-Segmentation Of Niemann-Pick Diseases Type C1, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Pharmacological Treatment
Gene Therapy
Substrate Reduction Therapy
Supportive Care
6.5. Global Niemann-Pick Disease Type C Treatment Market, Sub-Segmentation Of Niemann-Pick Diseases Type C2, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
Enzyme Replacement Therapy
Pharmacological Treatment
Gene Therapy
Supportive Care
7. Niemann-Pick Disease Type C Treatment Market Regional And Country Analysis
7.1. Global Niemann-Pick Disease Type C Treatment Market, Split By Region, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
7.2. Global Niemann-Pick Disease Type C Treatment Market, Split By Country, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
8. Asia-Pacific Niemann-Pick Disease Type C Treatment Market
8.1. Asia-Pacific Niemann-Pick Disease Type C Treatment Market Overview
Region Information, Market Information, Background Information, Government Initiatives, Regulations, Regulatory Bodies, Major Associations, Taxes Levied, Corporate Tax Structure, Investments, Major Companies
8.2. Asia-Pacific Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
8.3. Asia-Pacific Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
8.4. Asia-Pacific Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
9. China Niemann-Pick Disease Type C Treatment Market
9.1. China Niemann-Pick Disease Type C Treatment Market Overview
9.2. China Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion
9.3. China Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion
9.4. China Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion
10. India Niemann-Pick Disease Type C Treatment Market
10.1. India Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
10.2. India Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
10.3. India Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
11. Japan Niemann-Pick Disease Type C Treatment Market
11.1. Japan Niemann-Pick Disease Type C Treatment Market Overview
11.2. Japan Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
11.3. Japan Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
11.4. Japan Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
12. Australia Niemann-Pick Disease Type C Treatment Market
12.1. Australia Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
12.2. Australia Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
12.3. Australia Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
13. Indonesia Niemann-Pick Disease Type C Treatment Market
13.1. Indonesia Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
13.2. Indonesia Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
13.3. Indonesia Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
14. South Korea Niemann-Pick Disease Type C Treatment Market
14.1. South Korea Niemann-Pick Disease Type C Treatment Market Overview
14.2. South Korea Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
14.3. South Korea Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
14.4. South Korea Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
15. Western Europe Niemann-Pick Disease Type C Treatment Market
15.1. Western Europe Niemann-Pick Disease Type C Treatment Market Overview
15.2. Western Europe Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
15.3. Western Europe Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
15.4. Western Europe Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
16. UK Niemann-Pick Disease Type C Treatment Market
16.1. UK Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
16.2. UK Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
16.3. UK Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
17. Germany Niemann-Pick Disease Type C Treatment Market
17.1. Germany Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
17.2. Germany Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
17.3. Germany Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
18. France Niemann-Pick Disease Type C Treatment Market
18.1. France Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
18.2. France Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
18.3. France Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
19. Italy Niemann-Pick Disease Type C Treatment Market
19.1. Italy Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
19.2. Italy Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
19.3. Italy Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
20. Spain Niemann-Pick Disease Type C Treatment Market
20.1. Spain Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
20.2. Spain Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
20.3. Spain Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
21. Eastern Europe Niemann-Pick Disease Type C Treatment Market
21.1. Eastern Europe Niemann-Pick Disease Type C Treatment Market Overview
21.2. Eastern Europe Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
21.3. Eastern Europe Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
21.4. Eastern Europe Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
22. Russia Niemann-Pick Disease Type C Treatment Market
22.1. Russia Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
22.2. Russia Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
22.3. Russia Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
23. North America Niemann-Pick Disease Type C Treatment Market
23.1. North America Niemann-Pick Disease Type C Treatment Market Overview
23.2. North America Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
23.3. North America Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
23.4. North America Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
24. USA Niemann-Pick Disease Type C Treatment Market
24.1. USA Niemann-Pick Disease Type C Treatment Market Overview
24.2. USA Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
24.3. USA Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
24.4. USA Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
25. Canada Niemann-Pick Disease Type C Treatment Market
25.1. Canada Niemann-Pick Disease Type C Treatment Market Overview
25.2. Canada Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
25.3. Canada Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
25.4. Canada Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
26. South America Niemann-Pick Disease Type C Treatment Market
26.1. South America Niemann-Pick Disease Type C Treatment Market Overview
26.2. South America Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
26.3. South America Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
26.4. South America Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
27. Brazil Niemann-Pick Disease Type C Treatment Market
27.1. Brazil Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
27.2. Brazil Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
27.3. Brazil Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
28. Middle East Niemann-Pick Disease Type C Treatment Market
28.1. Middle East Niemann-Pick Disease Type C Treatment Market Overview
28.2. Middle East Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
28.3. Middle East Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
28.4. Middle East Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
29. Africa Niemann-Pick Disease Type C Treatment Market
29.1. Africa Niemann-Pick Disease Type C Treatment Market Overview
29.2. Africa Niemann-Pick Disease Type C Treatment Market, Segmentation By Disease Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
29.3. Africa Niemann-Pick Disease Type C Treatment Market, Segmentation By Age Group, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
29.4. Africa Niemann-Pick Disease Type C Treatment Market, Segmentation By End-User, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
30. Niemann-Pick Disease Type C Treatment Market Competitive Landscape And Company Profiles
30.1. Niemann-Pick Disease Type C Treatment Market Competitive Landscape
30.2. Niemann-Pick Disease Type C Treatment Market Company Profiles
30.2.1. Merck & Co. Inc. Overview, Products and Services, Strategy and Financial Analysis
30.2.2. Mayo Clinic Overview, Products and Services, Strategy and Financial Analysis
30.2.3. Boston Children's Hospital Overview, Products and Services, Strategy and Financial Analysis
30.2.4. Cincinnati Children's Hospital Medical Center Overview, Products and Services, Strategy and Financial Analysis
30.2.5. Mallinckrodt Pharmaceuticals Overview, Products and Services, Strategy and Financial Analysis
31. Niemann-Pick Disease Type C Treatment Market Other Major And Innovative Companies
31.1. Myriad Genetics Inc.
31.2. Rainbow Children's Hospital
31.3. CENTOGENE N.V.
31.4. The Florey Institute of Neuroscience and Mental Health
31.5. Insilico Medicine Inc.
31.6. National Organization for Rare Disorders (NORD)
31.7. Zevra Therapeutics Inc.
31.8. Azafaros A.G.
31.9. IntraBio Inc.
31.10. National Niemann-Pick Disease Foundation (NNPDF)
31.11. Bloomsbury Genetic Therapies Ltd.
31.12. CTD Holdings Inc.
31.13. Okklo Life Sciences
31.14. Vtesse Inc.
31.15. Cyclo Therapeutics Inc.
32. Global Niemann-Pick Disease Type C Treatment Market Competitive Benchmarking And Dashboard
33. Key Mergers And Acquisitions In The Niemann-Pick Disease Type C Treatment Market
34. Recent Developments In The Niemann-Pick Disease Type C Treatment Market
35. Niemann-Pick Disease Type C Treatment Market High Potential Countries, Segments and Strategies
35.1 Niemann-Pick Disease Type C Treatment Market In 2029 - Countries Offering Most New Opportunities
35.2 Niemann-Pick Disease Type C Treatment Market In 2029 - Segments Offering Most New Opportunities
35.3 Niemann-Pick Disease Type C Treatment Market In 2029 - Growth Strategies
35.3.1 Market Trend Based Strategies
35.3.2 Competitor Strategies
36. Appendix
36.1. Abbreviations
36.2. Currencies
36.3. Historic And Forecast Inflation Rates
36.4. Research Inquiries
36.5. The Business Research Company
36.6. Copyright And Disclaimer
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