Global PNH and aHUS Industry Growth and Trends Forecast to 2031

Summary

PNH and aHUS, both are extremely rare and genetic diseases. Due to PNH, destruction of red blood cells of a person occurs quite sooner than it should. It is an acquired hematopoietic stem cell disorder. Hematopoietic stem cells are developed in bone marrow and eventually turn into red blood cells, white blood cells and platelets. A person with PNH has some defected hematopoietic cells which create defective red blood cells. These defective cells are highly susceptible to premature destruction by the complement system. aHUS is a disorders in which blood clots are formed in small blood vessels throughout the body. TMA can lead to heart stroke, attack, kidney failure and death.

According to APO Research, The global PNH and aHUS market was estimated at US$ million in 2025 and is projected to reach a revised size of US$ million by 2031, witnessing a CAGR of xx% during the forecast period 2026-2031.

North American market for PNH and aHUS is estimated to increase from $ million in 2025 to reach $ million by 2031, at a CAGR of % during the forecast period of 2026 through 2031.

Asia-Pacific market for PNH and aHUS is estimated to increase from $ million in 2025 to reach $ million by 2031, at a CAGR of % during the forecast period of 2026 through 2031.

Europe market for PNH and aHUS is estimated to increase from $ million in 2025 to reach $ million by 2031, at a CAGR of % during the forecast period of 2026 through 2031.

The major global companies of PNH and aHUS include Alexion Pharmaceuticals, Alnylam Pharmaceuticals and Omeros Corporation, etc. In 2024, the world's top three vendors accounted for approximately % of the revenue.

Report Scope

This report aims to provide a comprehensive presentation of the global market for PNH and aHUS, with both quantitative and qualitative analysis, to help readers develop business/growth strategies, assess the market competitive situation, analyze their position in the current marketplace, and make informed business decisions regarding PNH and aHUS.

The PNH and aHUS market size, estimations, and forecasts are provided in terms of revenue ($ millions), considering 2024 as the base year, with history and forecast data for the period from 2020 to 2031. This report segments the global PNH and aHUS market comprehensively. Regional market sizes, concerning products by Type, by Application, and by players, are also provided. For a more in-depth understanding of the market, the report provides profiles of the competitive landscape, key competitors, and their respective market ranks. The report also discusses technological trends and new product developments.

Key Companies & Market Share Insights

In this section, the readers will gain an understanding of the key players competing. This report has studied the key growth strategies, such as innovative trends and developments, intensification of product portfolio, mergers and acquisitions, collaborations, new product innovation, and geographical expansion, undertaken by these participants to maintain their presence. Apart from business strategies, the study includes current developments and key financials. The readers will also get access to the data related to global revenue, gross margin by manufacturers for the period 2020-2025. This all-inclusive report will certainly serve the clients to stay updated and make effective decisions in their businesses.

PNH and aHUS Segment by Company

Alexion Pharmaceuticals
Alnylam Pharmaceuticals
Omeros Corporation

PNH and aHUS Segment by Type

Soliris
Ultomiris

PNH and aHUS Segment by Application

PNH
aHUS

PNH and aHUS Segment by Region

North America
United States
Canada
Mexico
Europe
Germany
France
U.K.
Italy
Russia
Spain
Netherlands
Switzerland
Sweden
Poland
Asia-Pacific
China
Japan
South Korea
India
Australia
Taiwan
Southeast Asia
South America
Brazil
Argentina
Chile
Middle East & Africa
Egypt
South Africa
Israel
Türkiye
GCC Countries

Key Drivers & Barriers

High-impact rendering factors and drivers have been studied in this report to aid the readers to understand the general development. Moreover, the report includes restraints and challenges that may act as stumbling blocks on the way of the players. This will assist the users to be attentive and make informed decisions related to business. Specialists have also laid their focus on the upcoming business prospects.

Reasons to Buy This Report

1. This report will help the readers to understand the competition within the industries and strategies for the competitive environment to enhance the potential profit. The report also focuses on the competitive landscape of the global PNH and aHUS market, and introduces in detail the market share, industry ranking, competitor ecosystem, market performance, new product development, operation situation, expansion, and acquisition. etc. of the main players, which helps the readers to identify the main competitors and deeply understand the competition pattern of the market.
2. This report will help stakeholders to understand the global industry status and trends of PNH and aHUS and provides them with information on key market drivers, restraints, challenges, and opportunities.
3. This report will help stakeholders to understand competitors better and gain more insights to strengthen their position in their businesses. The competitive landscape section includes the market share and rank (in value), competitor ecosystem, new product development, expansion, and acquisition.
4. This report stays updated with novel technology integration, features, and the latest developments in the market
5. This report helps stakeholders to gain insights into which regions to target globally
6. This report helps stakeholders to gain insights into the end-user perception concerning the adoption of PNH and aHUS.
7. This report helps stakeholders to identify some of the key players in the market and understand their valuable contribution.

Chapter Outline

Chapter 1: Introduces the report scope of the report, executive summary of global and regional market size and CAGR for the history and forecast period (2020-2025, 2026-2031). It offers a high-level view of the current state of the market and its likely evolution in the short to mid-term, and long term.
Chapter 2: Provides the analysis of various market segments by type, covering the market size and development potential of each market segment, to help readers find the blue ocean market in different market segments.
Chapter 3: Provides the analysis of various market segments by application, covering the market size and development potential of each market segment, to help readers find the blue ocean market in different downstream markets.
Chapter 4: Introduces the market dynamics, latest developments of the market, the driving factors and restrictive factors of the market, the challenges and risks faced by manufacturers in the industry, and the analysis of relevant policies in the industry.
Chapter 5: Detailed analysis of PNH and aHUS companies' competitive landscape, revenue, market share and ranking, latest development plan, merger, and acquisition information, etc.
Chapter 6: Provides profiles of key players, introducing the basic situation of the main companies in the market in detail, including product introduction, revenue, recent development, etc.
Chapter 7, 8, 9, 10 and 11: North America, Europe, Asia Pacific, South America, Middle East & Africa, revenue by country.
Chapter 12: Concluding Insights of the report

Please Note: Single-User license will be delivered via PDF from the publisher without the rights to print or to edit.


1 Market Overview

1.1 Product Definition
1.2 Global Market Growth Prospects
1.3 Global PNH and aHUS Market Size Overview by Region 2020 VS 2024 VS 2031
1.4 Global PNH and aHUS Market Size by Region (2020-2031)
1.4.1 Global PNH and aHUS Market Size by Region (2020-2025)
1.4.2 Global PNH and aHUS Market Size by Region (2026-2031)
1.5 Key Regions PNH and aHUS Market Size (2020-2031)
1.5.1 North America PNH and aHUS Market Size Growth Rate (2020-2031)
1.5.2 Europe PNH and aHUS Market Size Growth Rate (2020-2031)
1.5.3 Asia-Pacific PNH and aHUS Market Size Growth Rate (2020-2031)
1.5.4 South America PNH and aHUS Market Size Growth Rate (2020-2031)
1.5.5 Middle East & Africa PNH and aHUS Market Size Growth Rate (2020-2031)
2 PNH and aHUS Market by Type

2.1 Type Introduction
2.1.1 Soliris
2.1.2 Ultomiris
2.2 Global PNH and aHUS Market Size by Type
2.2.1 Global PNH and aHUS Market Size Overview by Type (2020-2031)
2.2.2 Global PNH and aHUS Historic Market Size Review by Type (2020-2025)
2.2.3 Global PNH and aHUS Market Size Forecasted by Type (2026-2031)
2.3 Global PNH and aHUS Market Size by Regions
2.3.1 North America PNH and aHUS Market Size Breakdown by Type (2020-2025)
2.3.2 Europe PNH and aHUS Market Size Breakdown by Type (2020-2025)
2.3.3 Asia-Pacific PNH and aHUS Market Size Breakdown by Type (2020-2025)
2.3.4 South America PNH and aHUS Market Size Breakdown by Type (2020-2025)
2.3.5 Middle East and Africa PNH and aHUS Market Size Breakdown by Type (2020-2025)
3 PNH and aHUS Market by Application

3.1 Type Introduction
3.1.1 PNH
3.1.2 aHUS
3.2 Global PNH and aHUS Market Size by Application
3.2.1 Global PNH and aHUS Market Size Overview by Application (2020-2031)
3.2.2 Global PNH and aHUS Historic Market Size Review by Application (2020-2025)
3.2.3 Global PNH and aHUS Market Size Forecasted by Application (2026-2031)
3.3 Global PNH and aHUS Market Size by Regions
3.3.1 North America PNH and aHUS Market Size Breakdown by Application (2020-2025)
3.3.2 Europe PNH and aHUS Market Size Breakdown by Application (2020-2025)
3.3.3 Asia-Pacific PNH and aHUS Market Size Breakdown by Application (2020-2025)
3.3.4 South America PNH and aHUS Market Size Breakdown by Application (2020-2025)
3.3.5 Middle East and Africa PNH and aHUS Market Size Breakdown by Application (2020-2025)
4 Global Market Dynamics

4.1 PNH and aHUS Industry Trends
4.2 PNH and aHUS Industry Drivers
4.3 PNH and aHUS Industry Opportunities and Challenges
4.4 PNH and aHUS Industry Restraints
5 Competitive Insights by Company

5.1 Global Top Players by PNH and aHUS Revenue (2020-2025)
5.2 Global PNH and aHUS Industry Company Ranking, 2023 VS 2024 VS 2025
5.3 Global PNH and aHUS Key Company Headquarters & Area Served
5.4 Global PNH and aHUS Company, Product Type & Application
5.5 Global PNH and aHUS Company Commercialization Time
5.6 Market Competitive Analysis
5.6.1 Global PNH and aHUS Market CR5 and HHI
5.6.2 Global Top 5 and 10 PNH and aHUS Players Market Share by Revenue in 2024
5.6.3 2024 PNH and aHUS Tier 1, Tier 2, and Tier 3
6 Company Profiles

6.1 Alexion Pharmaceuticals
6.1.1 Alexion Pharmaceuticals Comapny Information
6.1.2 Alexion Pharmaceuticals Business Overview
6.1.3 Alexion Pharmaceuticals PNH and aHUS Revenue, Global Share and Gross Margin (2020-2025)
6.1.4 Alexion Pharmaceuticals PNH and aHUS Product Portfolio
6.1.5 Alexion Pharmaceuticals Recent Developments
6.2 Alnylam Pharmaceuticals
6.2.1 Alnylam Pharmaceuticals Comapny Information
6.2.2 Alnylam Pharmaceuticals Business Overview
6.2.3 Alnylam Pharmaceuticals PNH and aHUS Revenue, Global Share and Gross Margin (2020-2025)
6.2.4 Alnylam Pharmaceuticals PNH and aHUS Product Portfolio
6.2.5 Alnylam Pharmaceuticals Recent Developments
6.3 Omeros Corporation
6.3.1 Omeros Corporation Comapny Information
6.3.2 Omeros Corporation Business Overview
6.3.3 Omeros Corporation PNH and aHUS Revenue, Global Share and Gross Margin (2020-2025)
6.3.4 Omeros Corporation PNH and aHUS Product Portfolio
6.3.5 Omeros Corporation Recent Developments
7 North America

7.1 North America PNH and aHUS Market Size Growth Rate (CAGR) by Country: 2020 VS 2024 VS 2031
7.2 North America PNH and aHUS Market Size by Country (2020-2025)
7.3 North America PNH and aHUS Market Size Forecast by Country (2026-2031)
8 Europe

8.1 Europe PNH and aHUS Market Size Growth Rate (CAGR) by Country: 2020 VS 2024 VS 2031
8.2 Europe PNH and aHUS Market Size by Country (2020-2025)
8.3 Europe PNH and aHUS Market Size Forecast by Country (2026-2031)
9 Asia-Pacific

9.1 Asia-Pacific PNH and aHUS Market Size Growth Rate (CAGR) by Country: 2020 VS 2024 VS 2031
9.2 Asia-Pacific PNH and aHUS Market Size by Country (2020-2025)
9.3 Asia-Pacific PNH and aHUS Market Size Forecast by Country (2026-2031)
10 South America

10.1 South America PNH and aHUS Market Size Growth Rate (CAGR) by Country: 2020 VS 2024 VS 2031
10.2 South America PNH and aHUS Market Size by Country (2020-2025)
10.3 South America PNH and aHUS Market Size Forecast by Country (2026-2031)
11 Middle East & Africa

11.1 Middle East & Africa PNH and aHUS Market Size Growth Rate (CAGR) by Country: 2020 VS 2024 VS 2031
11.2 Middle East & Africa PNH and aHUS Market Size by Country (2020-2025)
11.3 Middle East & Africa PNH and aHUS Market Size Forecast by Country (2026-2031)
12 Concluding Insights
13 Appendix

13.1 Reasons for Doing This Study
13.2 Research Methodology
13.3 Research Process
13.4 Authors List of This Report
13.5 Data Source
13.5.1 Secondary Sources
13.5.2 Primary Sources

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