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United States Gene Therapy Market Report 2018

Summary

The Gene Therapy are expected to grow at a CAGR of 112% from 428.5 million USD in 2018 to reach 84076.7 million USD by 2025 in United States market. In 2018, there are only four companies approved by FDA: Kite Pharma, BioVex, Novartis and Spark Therapeutics.

The major players in Gene Therapy market include
Kite Pharma
BioVex
Novartis
Spark Therapeutics

Geographically, this report is segmented into several key Regions, with revenue, market share and growth rate of Gene Therapy in these regions, from 2018 to 2025 (forecast), covering
The Northeast
The Midwest
The West
The South

On the basis of product, the Gene Therapy market is primarily split into
Ex Vivo
In Vivo

On the basis on the end users/applications, this report covers

Cancer Diseases
Hematological Disease
Hereditary Disease
Others


Table of Contents

1 Gene Therapy Overview 1
Product Overview and Scope of Gene Therapy 1
1.1.1 Product Overview 1
1.1.2 How does Gene Therapy work 1
1.2 Classification of Gene Therapy by Product Category 3
1.2.1 United States Gene Therapy Market Comparison by Types (2018-2025) 3
1.2.2 United States Gene Therapy Market Share by Types (Product Category) in 2018 4
1.2.3 Ex Vivo 5
1.2.4 In Vivo 6
1.3 United States Gene Therapy Market by Applications 7
1.3.1 United States Gene Therapy Revenue and Market Share Comparison by Applications (2018-2025) 7
1.3.2 Cancer Diseases 9
1.3.3 Hematological Disease 10
1.3.4 Hereditary Disease 11
1.4 United States Gene Therapy Market by Regions 11
1.4.1 United States Gene Therapy Market Size (M USD) Comparison by Regions (2018-2025) 12
1.4.2 The West Gene Therapy Status and Prospect (2018-2025) 12
1.4.3 The Midwest Gene Therapy Status and Prospect (2018-2025) 12
1.4.4 The Northeast Gene Therapy Status and Prospect (2018-2025) 13
1.4.5 The South Gene Therapy Status and Prospect (2018-2025) 14
1.5 United States Market Size of Gene Therapy (2018-2025) 15
1.6 Macroscopic Indicator 16
1.6.1 GDP for Major Regions 16
1.6.2 Population and Labor Considered for Forecast 18
1.6.3 Disposable Income Considered for Forecast 20
2 United States Gene Therapy Market Competition by Players/Manufacturers 22
2.1 United States Gene Therapy Revenue and Market Share of Key Players/Manufacturers (2018-2019) 22
2.2 United States Gene Therapy Gross Margin by Players/Manufacturers (2018-2019) 24
2.3 United States Gene Therapy Market Competitive Situation and Trends 25
2.3.1 United States Gene Therapy Market Concentration 25
2.3.2 United States Gene Therapy Market Share of Top 3 and Top 5 Players/Manufacturers 26
2.4 United States Players/Manufacturers Gene Therapy Headquarters and Established Date 26
by Regions (2018-2025) 27
3.1 United States Gene Therapy Revenue (M USD) and Market Share by Regions (2018-2025) 27
3.2 United States Gene Therapy Revenue Market Share by Regions (2018-2025) 28
4 United States Gene Therapy Revenue by Type/ Product Category (2018-2025) 33
4.1 United States Gene Therapy Revenue and Market Share by Type/ Product Category (2018-2025) 33
4.2 United States Gene Therapy Revenue and Growth Rate by Type (2018-2025) 36
5 United States Gene Therapy Revenue by Application (2018-2025) 38
5.1 United States Gene Therapy Revenue and Market Share by Applications (2018-2025) 38
5.2 United States Gene Therapy Revenue and Growth Rate by Applications (2018-2025) 42
6 Analysis of Gene Therapy Industry Key Manufacturers 45
6.1 Kite Pharma 45
6.1.1 Company Profile 45
6.1.2 Product Information 46
6.1.3 Revenue, Cost, Gross, and Gross Margin 49
6.2 BioVex 49
6.2.1 Company Profile 49
6.2.2 Product Information 50
6.2.3 Revenue, Cost, Gross, and Gross Margin 53
6.3 Novartis 53
6.3.1 Company Profile 53
6.3.2 Product Information 54
6.3.3 Revenue, Cost, Gross, and Gross Margin 55
6.4 Spark Therapeutics 56
6.4.1 Company Profile 56
6.4.2 Product Information 57
6.4.3 Revenue, Cost, Gross, and Gross Margin 58
7 USA Gene Therapy Research and Development Company Analysis 59
7.1 Bluebird Bio 59
7.1.1 Company Information 59
7.1.2 Gene Therapy Product Type and Technology 60
7.2 Sangamo 61
7.2.1 Company Information 61
7.2.2 Gene Therapy Product Type and Technology 62
7.3 Ultragenyx 63
7.3.1 Company Information 63
7.3.2 Gene Therapy Product Type and Technology 63
7.3.3 DTX 301 for OTC 64
7.3.4 DTX 401 for GSDIa 64
7.4 Avalanche Bio 65
7.4.1 Company Information 65
7.4.2 Gene Therapy Product Type and Technology 66
8 Gene Therapy Technology and Development Trend 67
8.1 Gene Therapy Technology Analysis 67
8.1.1 Gene Augmentation Therapy 70
8.1.2 Gene Inhibition Therapy 71
8.1.3 Killing of Specific Cells 72
8.2 Gene Therapy Technology Development Trend 73
9 Global Gene Therapy Trials Analysis 75
9.1 Global Gene Therapy Trials Analysis by Region 75
9.2 Global Gene Therapy Trials Analysis by Country 76
9.3 Global Gene Therapy Trials Analysis by Indications 77
9.4 Global Gene Therapy Trials Analysis by Gene Type 78
9.5 Global Gene Therapy Trials Analysis by Phases 80
9.6 Global Number of Gene Therapy Trials Approved 1989-2018.08 82
10 Factors Influencing 83
10.1 Price Trend of Key Industrial Raw Material 83
10.2 Interest Rate 84
10.3 Exports & Imports 85
11 Research Findings and Conclusion 89
12 Methodology and Data Source 90
12.1 Methodology/Research Approach 90
12.1.1 Research Programs/Design 90
12.1.2 Market Size Estimation 91
12.1.3 Market Breakdown and Data Triangulation 93
12.2 Data Source 94
12.2.1 Secondary Sources 94
12.2.2 Primary Sources 94
12.3 Author List 95
12.4 Disclaimer 96

 
List of Tables and Figures

Figure Product Picture of Gene Therapy 1
Figure Picture of Viruses Work 2
Figure Picture of the Process of Inserting the Vector in Gene Therapy 2
Table United States Gene Therapy Revenue (M USD) and Growth Rate Comparison by Types (Product Category) (2018-2025) 3
Figure United States Gene Therapy Revenue Market Share by Types (Product Category) in 2018 4
Figure the Procedure for Ex Vivo Gene Therapy 6
Figure Diagrammatic Representation of In Vivo Gene Therapy Product Picture 7
Table United States Gene Therapy Revenue (M USD) Comparison by Applications (2018-2025) 7
Figure United States Revenue Market Share of Gene Therapy by Applications in 2018 8
Figure Cancer Diseases Examples 9
Table Key Downstream Customer in Cancer Diseases 9
Figure Hematological Disease Examples 10
Table Key Downstream Customer in Hematological Disease 10
Figure Hereditary Disease Examples 11
Table Key Downstream Customer in Hereditary Disease 11
Figure The West Gene Therapy Revenue (M USD) and Growth Rate (2018-2025) 12
Figure The Midwest Gene Therapy Revenue (M USD) and Growth Rate (2018-2025) 13
Figure The Northeast Gene Therapy Revenue (M USD) and Growth Rate (2018-2025) 13
Figure The South Gene Therapy Revenue (M USD) and Growth Rate (2018-2025) 14
Figure United States Gene Therapy Revenue (M USD) and Growth Rate (2018-2025) 15
Figure GDP for Major Regions in 2016 16
Figure G20 GDP Long-Term Forecast Total, Million US dollars, 2060 17
Figure G20 Gross Domestic Product (GDP)Total, US Dollars/Capita, 2016 17
Figure Saving Rate Total, % of GDP, 2015 18
Figure Forecast of Global Middle-Class Population, 2015 to 2030 18
Figure Fertility Rates per Woman, 1970 to 2015 19
Figure Average Years of Schooling of the Adult Population 19
Figure Household Disposable Income Gross adjusted, US dollars/capita, 2016 20
Figure Household Spending Total, Million US dollars, 2015 20
Figure Net National Income Total, US dollars/capita, 2017 21
Table United States Gene Therapy Revenue of Key Players/Manufacturers (2018-2019) 22
Table United States Gene Therapy Revenue Share by Players/Manufacturers (2018-2019) 22
Figure 2018 United States Gene Therapy Revenue Share by Players/Manufacturers 23
Figure 2019 United States Gene Therapy Revenue Share by Players/Manufacturers 23
Table United States Gene Therapy Gross Margin by Players/Manufacturers (2018-2019) 24
Figure 2018 United States Gene Therapy Revenue (M USD) by Players/Manufacturers 25
Figure United States Gene Therapy Market Share of Top 3 Players/Manufacturers 26
Table United States Players/Manufacturers Gene Therapy Headquarters and Established Date 26
Table United States Gene Therapy Revenue (M USD) by Regions (2018-2025) 27
Table United States Gene Therapy Revenue Share by Regions (2018-2025) 27
Figure United States Gene Therapy Revenue Share by Regions (2018-2025) 28
Figure United States Gene Therapy Revenue Market Share by Regions in 2018 28
Figure United States Gene Therapy Revenue Market Share by Regions in 2019 29
Figure United States Gene Therapy Revenue Market Share by Regions in 2020 29
Figure United States Gene Therapy Revenue Market Share by Regions in 2021 30
Figure United States Gene Therapy Revenue Market Share by Regions in 2022 30
Figure United States Gene Therapy Revenue Market Share by Regions in 2023 31
Figure United States Gene Therapy Revenue Market Share by Regions in 2024 31
Figure United States Gene Therapy Revenue Market Share by Regions in 2025 32
Table United States Gene Therapy Revenue (M USD) by Type (2018-2025) 33
Table United States Gene Therapy Revenue Share by Type (2018-2025) 33
Figure United States Gene Therapy Revenue Share by Type (2018-2025) 34
Figure United States Gene Therapy Revenue Market Share by Type in 2018 34
Figure United States Gene Therapy Revenue Market Share by Type in 2025 35
Figure United States Ex Vivo Gene Therapy Revenue (M USD) and Growth Rate by Type (2018-2025) 36
Figure United States In Vivo Gene Therapy Revenue and Growth Rate by Type (2018-2025) 37
Table United States Gene Therapy Revenue (M USD) by Applications (2018-2025) 38
Table United States Gene Therapy Revenue Market Share by Applications (2018-2025) 38
Figure United States Gene Therapy Revenue Market Share by Applications (2018-2025) 39
Figure United States Gene Therapy Revenue Market Share by Applications in 2018 40
Figure United States Gene Therapy Revenue Market Share by Applications in 2025 41
Figure United States Gene Therapy in Cancer Diseases Revenue (M USD) and Growth Rate by Applications (2018-2025) 42
Figure United States Gene Therapy in Hematological Disease Revenue (M USD) and Growth Rate by Applications (2018-2025) 43
Figure United States Gene Therapy in Hereditary Disease Revenue (M USD) and Growth Rate by Applications (2018-2025) 44
Table Kite Pharma Company Profile 45
Table YESCARTA 6 Distinct Steps 47
Table Results with Yescarta 48
Figure Results with Yescarta 48
Table Gene Therapy Cost (M USD), Gross (M USD), Revenue (M USD) and Gross Margin of Kite Pharma 2018-2019 49
Table BioVex Company Profile 49
Table IMLYGIC Works 51
Table Imlygic injected into 3 kinds of Melanoma Tumors 52
Figure IMLYGIC Treatment 52
Table Gene Therapy Cost (M USD), Gross (M USD), Revenue (M USD) and Gross Margin of BioVex 2018-2019 53
Table Novartis Company Profile 53
Figure KYMRIAH Mechanism of Action 54
Table Gene Therapy Cost (M USD), Gross (M USD), Revenue (M USD) and Gross Margin of Novartis 2018-2019 55
Table Spark Therapeutics Company Profile 56
Table Gene Therapy Cost (M USD), Gross (M USD), Revenue (M USD) and Gross Margin of Spark Therapeutics 2018-2019 58
Table Bluebird Bio Basic Information List 59
Figure Program Pipeline 60
Table Sangamo Basic Information List 61
Figure Product Pipeline 62
Table Ultragenyx Basic Information List 63
Figure Product Pipeline 63
Table Avalanche Bio Basic Information List 65
Figure Programs Pipeline 66
Figure Partnered Programs Pipeline 66
Table Characteristic Diseases Caused by Gene Mutations that Code these Products 67
Table Human Gene Therapy Trials Conducted 68
Table Challenges of Gene Therapy 69
Table Key Facts of Gene Augmentation Therapy 70
Figure Gene Augmentation Therapy 71
Table Key Facts of Gene Augmentation Therapy 71
Figure Gene Inhibition Therapy 72
Table Key Facts of Killing of Specific Cells 72
Figure Killing of Specific Cells 73
Table Gene Therapy Trials Analysis by Region 75
Figure Gene Therapy Trials Distribution by Region 75
Table Gene Therapy Trials Analysis by Country 76
Figure Gene Therapy Trials Distribution by Country 77
Table Gene Therapy Trials Analysis by Indications 77
Figure Gene Therapy Trials Distribution by Indications 78
Table Gene Therapy Trials Analysis by Gene Type 78
Figure Gene Therapy Trials Distribution by Gene Type 80
Table Gene Therapy Trials Analysis by Phases 80
Figure Gene Therapy Trials Distribution by Phases 81
Figure Global Number of Gene Therapy Trials Approved 1989-2018.08 82
Figure Price Trend of Crude Oil (USD/BBL) 83
Figure Price Trend of Brent Crude Oil (USD/BBL) 83
Figure Price Trend of Natural Gas (MMBtu) 84
Figure Price Trend of Gasoline (GAL) 84
Figure United States Fed Funds Rate 84
Figure USD LIBOR Three-Month Rate 85
Figure United States Imports 85
Figure United States¡¯ Import by Category 86
Figure United States¡¯ Import by Origin 87
Figure United States Exports by Category 87
Figure United States Exports by Destination 88
Table Research Programs/Design for This Report 90
Figure Bottom-up and Top-down Approaches for This Report 92
Figure Data Triangulation 93
Table Key Data Information from Secondary Sources 94
Table Key Data Information from Primary Sources 95

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