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Global Krabbe Disease Treatment Market 2018-2022

Global Krabbe Disease Treatment Market 2018-2022

About Krabbe Disease Treatment

Krabbe disease is a rare inherited genetic disorder that affects the nervous system. It is usually caused by the deficiency of the galactosylceramidase (GLC) enzyme. The disease is inherited in an autosomal recessive pattern.

Technavio’s analysts forecast the global krabbe disease treatment market to grow at a CAGR of 7.24% during the period 2018-2022.

Covered in this report

The report covers the present scenario and the growth prospects of the global krabbe disease treatment market for 2018-2022. To calculate the market size, the report presents a detailed picture of the market by way of study, synthesis, and summation of data from multiple sources.

The market is divided into the following segments based on geography:

  • Americas
  • APAC
  • EMEA
Technavio's report, Global Krabbe Disease Treatment Market 2018-2022, has been prepared based on an in-depth market analysis with inputs from industry experts. The report covers the market landscape and its growth prospects over the coming years. The report also includes a discussion of the key vendors operating in this market.

Key vendors
  • GlaxoSmithKline
  • Johnson & Johnson
  • Novartis
Market driver
  • Special drug designation
  • For a full, detailed list, view our report
Market challenge
  • Limited patient pool for clinical trials
  • For a full, detailed list, view our report
Market trend
  • Emergence of pharmacological chaperone therapy
  • For a full, detailed list, view our report
Key questions answered in this report
  • What will the market size be in 2022 and what will the growth rate be?
  • What are the key market trends?
  • What is driving this market?
  • What are the challenges to market growth?
  • Who are the key vendors in this market space?


Press Release

Technavio Announces the Publication of its Research Report – Global Krabbe Disease Treatment Market 2018-2022

Technavio recognizes the following companies as the key players in the global krabbe disease treatment market: GlaxoSmithKline, Johnson & Johnson, and Novartis.

Commenting on the report, an analyst from Technavio’s team said: “One trend in the market is emergence of pharmacological chaperone therapy. More than two-fifth known cases of Krabbe disease are due to missense mutation in the GLC enzyme. Such mutations result in the disruption of enzyme folding and ultimately stops the GLC from reaching its site of action in enough amounts in the lysosome.”

According to the report, one driver in the market is special drug designation. An important factor that is expected to drive market growth is the assignment of special drug designations to drugs and biologics that are intended for the safe and effective treatment of Krabbe disease. The priority review program for facilitating fast drug approvals is offered by the Food and Drug Administration (FDA).

Further, the report states that one challenge in the market is limited patient pool for clinical trials. The prevalence rate of orphan diseases such as Krabbe is very low. Therefore, the percentage of population affected by such diseases is also low in comparison with other disorders. This, in turn, restricts the number of patients available for clinical trial evaluation of drugs under development for the treatment of orphan diseases.

Companies Mentioned

GlaxoSmithKline, Johnson & Johnson, and Novartis.

  • Executive summary
  • Scope of the report
  • Research methodology
  • Introduction
    • Market outline
    • Types of Krabbe disease
      • Table Types of Krabbe disease
  • Market landscape
    • Market ecosystem
      • Table Parent market
      • Table Global rare diseases treatment market: Segmentation
    • Market characteristics
      • Table Market characteristics
    • Market segmentation analysis
      • Table Market segments
  • Market sizing
    • Market definition
      • Table Market definition: Inclusions and exclusions checklist
    • Market sizing
      • Table Market size
      • Table Validation techniques employed for market sizing 2017
    • Market size and forecast
      • Table Global Krabbe disease treatment market 2017-2022 ($ millions)
      • Table Global Krabbe disease treatment market: Year over year growth 2018-2022 (%)
  • Five forces analysis
    • Table Five forces analysis 2017
    • Table Five forces analysis 2022
    • Bargaining power of buyers
      • Table Bargaining power of buyers
    • Bargaining power of suppliers
      • Table Bargaining power of suppliers
    • Threat of new entrants
      • Table Threat of new entrants
    • Threat of substitutes
      • Table Threat of substitutes
    • Threat of rivalry
      • Table Threat of rivalry
    • Market condition
  • Pipeline analysis
    • Table Pipeline landscape by development phase
    • Table Key clinical trials for global Krabbe disease treatment market
  • Market segmentation by therapy
    • Segmentation by therapy
      • Table Global Krabbe disease treatment market by therapy 2017-2022 (% share)
    • Comparison by therapy
      • Table Comparison by therapy
    • Global Krabbe disease treatment market by anticonvulsants
      • Table Global Krabbe disease treatment market by anticonvulsants 2017-2022 ($ millions)
      • Table Global Krabbe disease treatment market by anticonvulsants: Year over year growth 2018-2022 (%)
    • Global Krabbe disease treatment market by muscle relaxants
      • Table Global Krabbe disease treatment market by muscle relaxants 2017-2022 ($ millions)
      • Table Global Krabbe disease treatment market by muscle relaxants: Year over year growth 2018-2022 (%)
    • Global Krabbe disease treatment market by HSCT
      • Table Global Krabbe disease treatment market by HSCT 2017-2022 ($ millions)
      • Table Global Krabbe disease treatment market by HSCT: Year over year growth 2018-2022 (%)
    • Global Krabbe disease treatment market by others
      • Table Global Krabbe disease treatment market by others 2017-2022 ($ millions)
      • Table Global Krabbe disease treatment market by others: Year over year growth 2018-2022 (%)
    • Market opportunity by therapy
      • Table Market opportunity by therapy
  • Customer landscape
    • Table Customer landscape
  • Regional landscape
    • Geographical segmentation
      • Table Global Krabbe disease treatment market by region 2017-2022 (% share)
    • Regional comparison
      • Table Regional comparison
    • Krabbe disease treatment market in Americas
      • Table Krabbe disease treatment market in Americas 2017-2022 ($ millions)
      • Table Krabbe disease treatment market in Americas: Year over year growth 2018-2022 (%)
    • Krabbe disease treatment market in EMEA
      • Table Krabbe disease treatment market in EMEA 2017-2022 ($ millions)
      • Table Krabbe disease treatment market in EMEA: Year over year growth 2018-2022 (%)
    • Krabbe disease treatment market in APAC
      • Table Krabbe disease treatment market in APAC 2017-2022 ($ millions)
      • Table Krabbe disease treatment market in APAC: Year over year growth 2018-2022 (%)
    • Key leading countries
      • Table Key leading countries
    • Market opportunity
      • Table Market opportunity
  • Decision framework
  • Drivers and challenges
    • Market drivers
    • Market challenges
      • Table Some long-term complications in HSCT patients
  • Market trends
    • Emergence of pharmacological chaperone therapy
    • Gene technology in therapy
  • Vendor landscape
    • Overview
      • Table Vendor landscape
    • Landscape disruption
      • Table Landscape disruption
  • Vendor analysis
    • Vendors covered
      • Table Vendors covered
    • Vendor classification
      • Table Vendor classification
    • Market positioning of vendors
      • Table Market positioning of vendors
    • GlaxoSmithKline
      • Table GlaxoSmithKline: Overview
      • Table GlaxoSmithKline: Business segments
      • Table GlaxoSmithKline: Organizational developments
      • Table GlaxoSmithKline: Geographic focus
      • Table Johnson & Johnson: Segment focus
      • Table GlaxoSmithKline: Key offerings
      • Table GlaxoSmithKline: Key customers
    • Johnson & Johnson
      • Table Johnson & Johnson: Overview
      • Table Johnson & Johnson: Business segments
      • Table Johnson & Johnson: Organizational developments
      • Table Johnson & Johnson: Geographic focus
      • Table Johnson & Johnson: Segment focus
      • Table Johnson & Johnson: Key offerings
      • Table Johnson & Johnson: Key customers
    • Novartis
      • Table Novartis: Overview
      • Table Novartis: Business segments
      • Table Novartis: Organizational developments
      • Table Novartis: Geographic focus
      • Table Novartis: Segment focus
      • Table Novartis: Key offerings
      • Table Novartis: Key customers
  • Appendix
    • List of abbreviations
  • Explore Technavio

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